{"id":324213,"date":"2020-09-30T10:25:20","date_gmt":"2020-09-30T14:25:20","guid":{"rendered":"https:\/\/patientworthy.wpengine.com\/2020\/09\/30\/actualizaciones-sobre-el-tratamiento-de-la-distrofia-muscular-de-duchenne\/"},"modified":"2020-09-30T10:25:28","modified_gmt":"2020-09-30T14:25:28","slug":"actualizaciones-sobre-el-tratamiento-de-la-distrofia-muscular-de-duchenne","status":"publish","type":"post","link":"https:\/\/patientworthy.com\/es\/2020\/09\/30\/actualizaciones-sobre-el-tratamiento-de-la-distrofia-muscular-de-duchenne\/","title":{"rendered":"Actualizaciones Sobre el Tratamiento de la Distrofia Muscular de Duchenne"},"content":{"rendered":"<p>Sarepta Therapeutics se ha reunido con la Oficina de Tejidos y Terapias Avanzadas de la FDA para discutir una respuesta escrita de Tipo C sobre un ensayo cl\u00ednico para SRP-9001, un tratamiento de la distrofia muscular de Duchenne.<\/p>\n<h2>Acerca de la Distrofimuscular de Duchenne (DMD)<\/h2>\n<p><a href=\"https:\/\/patientworthy.com\/duchenne-muscular-dystrophy-dmd\/\">La distrofia muscular de Duchenne<\/a> es una de las nueve formas de distrofia muscular. Las personas afectadas experimentan debilidad muscular progresiva y atrofia debido a la falta de distrofina. Los s\u00edntomas incluyen problemas con las habilidades motoras, debilidad muscular, ca\u00eddas, fatiga, problemas para cambiar de posici\u00f3n, problemas para caminar, problemas de aprendizaje y, finalmente, enfermedades card\u00edacas e insuficiencia respiratoria. Todos estos efectos son causados por una mutaci\u00f3n transmitida en el cromosoma X en un patr\u00f3n recesivo. Actualmente no existe cura para esta afecci\u00f3n, pero los tratamientos pueden ayudar a controlar los s\u00edntomas.<\/p>\n<h2>Actualizaciones en SRP-9001<\/h2>\n<p>Sarepta tuvo que reunirse con la FDA para recibir su consentimiento al comienzo de su pr\u00f3ximo ensayo cl\u00ednico de SRP-9001, una terapia de transferencia gen\u00e9tica, ya que quieren utilizar material de proceso comercial.<\/p>\n<p>En esta reuni\u00f3n, la FDA solicit\u00f3 que haya otro ensayo de potencia para su liberaci\u00f3n antes de que se administre la dosis a los participantes. Si bien Sarepta ya tiene datos sobre ensayos de potencia, es necesario que haya m\u00e1s di\u00e1logo para averiguar si estos datos pueden usarse.<\/p>\n<p>Hubo otras solicitudes de la FDA, y Sarepta se complace en trabajar con ellos para brindar el mejor tratamiento posible a las personas con distrofia muscular de Duchenne.<\/p>\n<p>Lea el art\u00edculo fuente <a href=\"https:\/\/www.biospace.com\/article\/releases\/sarepta-therapeutics-provides-program-update-for-srp-9001-its-investigational-gene-therapy-for-the-treatment-of-duchenne-muscular-dystrophy\/\">aqu\u00ed<\/a>.<\/p>\n","protected":false},"excerpt":{"rendered":"<p>Sarepta Therapeutics se ha reunido con la Oficina de Tejidos y Terapias Avanzadas de la FDA para discutir una respuesta escrita de Tipo C sobre un ensayo cl\u00ednico para SRP-9001, un tratamiento de la distrofia muscular de Duchenne. Acerca de la Distrofimuscular de Duchenne (DMD) La distrofia muscular de Duchenne es una de las nueve [&hellip;]<\/p>\n","protected":false},"author":1025,"featured_media":324214,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"ocean_front_end_style_editor":"no","ocean_post_layout":"","ocean_both_sidebars_style":"","ocean_both_sidebars_content_width":0,"ocean_both_sidebars_sidebars_width":0,"ocean_sidebar":"0","ocean_second_sidebar":"0","ocean_disable_margins":"enable","ocean_add_body_class":"","ocean_shortcode_before_top_bar":"","ocean_shortcode_after_top_bar":"","ocean_shortcode_before_header":"","ocean_shortcode_after_header":"","ocean_has_shortcode":"","ocean_shortcode_after_title":"","ocean_shortcode_before_footer_widgets":"","ocean_shortcode_after_footer_widgets":"","ocean_shortcode_before_footer_bottom":"","ocean_shortcode_after_footer_bottom":"","ocean_display_top_bar":"default","ocean_display_header":"default","ocean_header_style":"","ocean_center_header_left_menu":"0","ocean_custom_header_template":"0","ocean_custom_logo":0,"ocean_custom_retina_logo":0,"ocean_custom_logo_max_width":0,"ocean_custom_logo_tablet_max_width":0,"ocean_custom_logo_mobile_max_width":0,"ocean_custom_logo_max_height":0,"ocean_custom_logo_tablet_max_height":0,"ocean_custom_logo_mobile_max_height":0,"ocean_header_custom_menu":"0","ocean_menu_typo_font_family":"0","ocean_menu_typo_font_subset":"","ocean_menu_typo_font_size":0,"ocean_menu_typo_font_size_tablet":0,"ocean_menu_typo_font_size_mobile":0,"ocean_menu_typo_font_size_unit":"px","ocean_menu_typo_font_weight":"","ocean_menu_typo_font_weight_tablet":"","ocean_menu_typo_font_weight_mobile":"","ocean_menu_typo_transform":"","ocean_menu_typo_transform_tablet":"","ocean_menu_typo_transform_mobile":"","ocean_menu_typo_line_height":0,"ocean_menu_typo_line_height_tablet":0,"ocean_menu_typo_line_height_mobile":0,"ocean_menu_typo_line_height_unit":"","ocean_menu_typo_spacing":0,"ocean_menu_typo_spacing_tablet":0,"ocean_menu_typo_spacing_mobile":0,"ocean_menu_typo_spacing_unit":"","ocean_menu_link_color":"","ocean_menu_link_color_hover":"","ocean_menu_link_color_active":"","ocean_menu_link_background":"","ocean_menu_link_hover_background":"","ocean_menu_link_active_background":"","ocean_menu_social_links_bg":"","ocean_menu_social_hover_links_bg":"","ocean_menu_social_links_color":"","ocean_menu_social_hover_links_color":"","ocean_disable_title":"default","ocean_disable_heading":"default","ocean_post_title":"","ocean_post_subheading":"","ocean_post_title_style":"","ocean_post_title_background_color":"","ocean_post_title_background":0,"ocean_post_title_bg_image_position":"","ocean_post_title_bg_image_attachment":"","ocean_post_title_bg_image_repeat":"","ocean_post_title_bg_image_size":"","ocean_post_title_height":0,"ocean_post_title_bg_overlay":0.5,"ocean_post_title_bg_overlay_color":"","ocean_disable_breadcrumbs":"default","ocean_breadcrumbs_color":"","ocean_breadcrumbs_separator_color":"","ocean_breadcrumbs_links_color":"","ocean_breadcrumbs_links_hover_color":"","ocean_display_footer_widgets":"default","ocean_display_footer_bottom":"default","ocean_custom_footer_template":"0","ocean_post_oembed":"","ocean_post_self_hosted_media":"","ocean_post_video_embed":"","ocean_link_format":"","ocean_link_format_target":"self","ocean_quote_format":"","ocean_quote_format_link":"post","ocean_gallery_link_images":"on","ocean_gallery_id":[]},"categories":[12164,12074],"tags":[12366,12168,12076,19041,14398],"_links":{"self":[{"href":"https:\/\/patientworthy.com\/es\/wp-json\/wp\/v2\/posts\/324213"}],"collection":[{"href":"https:\/\/patientworthy.com\/es\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/patientworthy.com\/es\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/patientworthy.com\/es\/wp-json\/wp\/v2\/users\/1025"}],"replies":[{"embeddable":true,"href":"https:\/\/patientworthy.com\/es\/wp-json\/wp\/v2\/comments?post=324213"}],"version-history":[{"count":0,"href":"https:\/\/patientworthy.com\/es\/wp-json\/wp\/v2\/posts\/324213\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/patientworthy.com\/es\/wp-json\/wp\/v2\/media\/324214"}],"wp:attachment":[{"href":"https:\/\/patientworthy.com\/es\/wp-json\/wp\/v2\/media?parent=324213"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/patientworthy.com\/es\/wp-json\/wp\/v2\/categories?post=324213"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/patientworthy.com\/es\/wp-json\/wp\/v2\/tags?post=324213"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}