Patient Worthy – Page 9

Metabolic dysfunction-associated steatohepatitis

Madrigal Pharmaceuticals’ REZDIFFRA Shines as GLP-1 Drugs Approach the MASH Market

Bree Clare - June 30, 2025

Huntington's Disease

A Promising Spark: First Huntington’s Disease Patient Dosed in Roche Gene Therapy Trial

Dravet Syndrome

Camp Small Steps Helps Dravet Syndrome Families Find Community and Connection

Anixa Biosciences Advances CAR-T Therapy: First Patient Dosed in Fourth Clinical Trial Cohort

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Meet Gabby: The Shield-maiden With the Sweetest Hugs

Reducing the Itch: Life with Progressive Familial Intrahepatic Cholestasis (PFIC)

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We Need Equity and Diversity Within Rare Disease Research

Bridging the Diversity Gap in Healthcare

Rare Disease Clinical Trials Are Essential to Help Uncover Potential Patient Solutions: Spotlight on Classic Congenital Adrenal Hyperplasia (CAH)

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Arthrogryposis, also known as Arthrogryposis Multi

The whole future lies in uncertainty: live immedia

Anixa, the group behind CAR-T therapy, has reached

Alzheimer's disease is more than memory loss. It p

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Thanks to organ donation, this 10-year-old has bee

Meet Kayleigh a caregiver to her son living with D

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A breakthrough has been achieved in a clinical stu

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