Chronic Kidney Disease
Some Dialysis Humor, Part 2
Editor’s Note: This is part 2 of a 3-part caregiver story, submitted to us by Joan Foster, who was a caregiver for her husband Charles’
Repairing the Wiring: How a New Stem Cell Therapy Aims to Defeat Chronic Spinal Cord Injury
Huyabio’s HBI-8000 and Opdivo Combination Shows Significant Benefit in Phase 3 Melanoma Study
Megan’s Myasthenia Gravis Story: From Uncertainty to Advocacy
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Major Depressive Disorder
AtaiBeckley Completes Patient Dosing in Phase 2b Trial of VLS-01 for Treatment-Resistant Depression
As reported on PharmaBiz, AtaiBeckley has announced a key milestone in the development of its investigational depression therapy, VLS-01, with the final participant now dosed
Generalized arterial calcification of infancy-1 (GACI1)
Natalie’s GACI Story
Editor’s Note: Patient Worthy is honored to share this story, originally written by Anne and Jerry van Wyk, and shared with us by our friends
Rare Disease
“Two Rare Diagnoses, One Common Lesson: Start with Genetic Testing”
Every day, parents just like me sit in doctors’ offices searching for answers. They know something isn’t quite right. Maybe their child isn’t meeting milestones.
Mesothelioma
New Experimental Drug Offers Hope for Mesothelioma Patients
As reported on Vermont Biz, researchers at the University of Vermont (UVM) and biotechnology company RS Oncology have reported encouraging results from an early-stage clinical
Alzheimer's disease
2026 Alzheimer’s Update
For more than a century Alzheimer’s disease has been thought to be incurable. But a recent study published in the New England Journal of Medicine
Chronic Kidney Disease
Some Dialysis Humor, Part 1
Editor’s Note: This is part 1 of a 3-part caregiver story, submitted to us by Joan Foster, who was a caregiver for her husband Charles’
Hepatocellular Carcinoma
FDA Issues Complete Response Letter for Rivoceranib–Camrelizumab Combination in Advanced Liver Cancer
As reported by The Manila Times, the U.S. Food and Drug Administration (FDA) has issued a Complete Response Letter (CRL) to Elevar Therapeutics regarding its
Hemophilia A
ISTH 2026: Long-Term Phase 3 Data Support Denecimig as a Flexible Prophylactic Option for Hemophilia A
As covered by Fairfax Times, Novo Nordisk has reported encouraging long-term findings for its investigational hemophilia A therapy denecimig (Mim8), with interim results from the
Rare Disease
Heal Canada’s Summer 2026 Issue of E3 Advocacy Magazine
Our friends at Heal Canada have launched the newest edition of their magazine, E3 Advocacy! Their digital publication focuses on the importance of patient advocacy,
Rare Disease
FDA Grants Breakthrough Device Designation to Aurenar’s V-Link System for Preventing Cerebral Vasospasm After Brain Hemorrhage
As reported on MobiHealth News, the U.S. Food and Drug Administration (FDA) has awarded Breakthrough Device designation to Aurenar’s V-Link System, a noninvasive neuromodulation technology
Congenital Adrenal Hyperplasia
An Interview with Allyson, a Congenital Adrenal Hyperplasia Patient
Can you take me back to when you first became aware that you had a health condition as a child. Did you overhear the adults
HIV/AIDS
Merck Partners With ACTF to Expand Access to New HIV Treatment Through State ADAP Programs
As reported on PharmaBiz, Merck has announced a new agreement with the ADAP Crisis Task Force (ACTF) aimed at improving access to its recently approved
Hidradenitis suppurativa
GLP-1 Receptor Agonists Associated With Lower Cardiovascular and Inflammatory Risks in Hidradenitis Suppurativa
As reported on MedPage Today, large retrospective study suggests that glucagon-like peptide-1 (GLP-1) receptor agonists may offer broad health benefits for patients with hidradenitis suppurativa
Duchenne Muscular Dystrophy
FDA Sets Early 2027 Review Deadline for Sarepta’s Duchenne Exon-Skipping Therapies Despite Confirmatory Trial Setback
As reported on BioSpace, Sarepta Therapeutics has reached an important regulatory milestone in its effort to secure traditional FDA approval for two Duchenne muscular dystrophy
Pompe Disease
Nexviazyme Achieves Key Phase 3 Milestone in Infants With Pompe Disease, Sanofi Prepares FDA Expansion Filing
As reported on Tech Times, Sanofi has reported positive results from its Phase 3 Baby-COMET study evaluating Nexviazyme (avalglucosidase alfa) in infants with infantile-onset Pompe
Ovarian Cancer
A Doctor-Patient Interview on Ovarian Cancer
Editor’s Note: Patient Worthy is honored to share this interview, featuring Kate, an ovarian cancer survivor, and Dr. Premal Thaker, M.D. “There is fear, and
Rare Disease
FDA Clears Orca Bio’s Tregzi for Adults Undergoing Allogeneic Stem Cell Transplantation for Blood Cancers
As reported on PharmaBiz, the US Food and Drug Administration (FDA) has approved Orca Bio’s Tregzi, a precision-engineered cell therapy designed for use in matched-donor
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Diagnosing gastric (stomach) and gastroesophageal junction (GEJ) cancer involves more than a single test. Healthcare providers often use a combination of endoscopy, biopsy, imaging, blood work, and staging to better understand what's happening and guide the next steps in care.
Understanding the diagnostic process can help reduce uncertainty and empower patients and caregivers to ask informed questions. Every diagnosis begins with gathering the right information—and every step plays an important role in creating a personalized treatment plan.
Click the link below to share your story today!
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#GastricCancer #stomachcancer #PatientWorthy
Sarcoma Awareness Month is observed each year in July to raise awareness of sarcoma, a rare group of cancers that develop in the bones or soft tissues of the body, including muscle, fat, blood vessels, nerves, tendons, and connective tissue.
The goals of Sarcoma Awareness Month include:
• Increasing public awareness and education about sarcoma.
• Encouraging earlier recognition and diagnosis.
• Supporting patients, survivors, caregivers, and families.
• Advocating for increased research funding and improved treatment options.
• Amplifying patient stories and experiences.
Because sarcoma is considered rare, it is often misdiagnosed or diagnosed later than more common cancers. Awareness efforts help educate healthcare providers and the public about symptoms, the importance of specialized care, and the need for continued research.
#SarcomaAwarenessMonth #sarcomaawareness #sarcoma #rarecancer #cancerawareness #patientadvocacy #PatientVoice #caregiversupport #shareyourstory #PatientWorthy 💛
The people who make the biggest difference aren't always the ones with all the answers.
Living with a chronic illness or rare disease often changes the way you see the people around you. It highlights the ones who listen, check in, remember the little things, and continue showing up through every high and low.
Sometimes, the smallest acts of support leave the biggest impact!
#ChronicIllness #raredisease #chronicillnessawareness #rarediseaseawareness #invisibleillness #youarenotalone #PatientWorthy
