Myelofibrosis
James’ Story: Navigating Life With Myelofibrosis
Editor’s Note: This article was shared with us by our friends at Heal Canada. To see the article in its original format, please click here.
Aardvark Pauses Late‑Stage Prader–Willi Trial After Cardiac Signals Emerge
- March 6, 2026
Myth or Truth? Avoid Soy If You Have a Hormone-Positive Cancer
Breaking New Ground: FDA Green-Lights Novel Breast Cancer Treatment Targeting Treatment-Resistant Tumors
Vico Therapeutics Begins Twice‑Yearly Dosing of VO659 in Phase 1/2 Trial for Huntington’s Disease and Spinocerebellar Ataxias
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THE LATEST FROM PATIENT WORTHY
Chronic Lymphocytic Leukemia
FDA Approves Revolutionary Oral Combination Therapy for Chronic Lymphocytic Leukemia, Offering Patients Freedom from Long-Term Treatment
AbbVie has announced a landmark regulatory milestone with the US FDA’s approval of a supplemental new drug application (sNDA) for the combination of Venclexta (venetoclax)
Rare Disease
First Patient Dosed in Phase 3 CLARITY Trial Evaluating Solriamfetol for MDD With Excessive Daytime Sleepiness
As published in Sleep Review Magazine, Axsome Therapeutics has officially begun dosing patients in its Phase 3 CLARITY trial, a study designed to evaluate solriamfetol
Fibrosis
Breaking the Fibrosis Barrier: How Fibrocor Therapeutics Is Revolutionizing Kidney Disease Treatment
Fibrosis, the accumulation of scar tissue in organs, disrupts normal organ function and leads to progressive impairment. Currently, there is no cure, and existing treatments
Diabetes Type 1
A New Chapter in Diabetes Care: Inside-the-Body Technology Breaks Ground
The relationship between people with type 1 diabetes and their medication has always been complicated. For decades, managing the condition has required constant vigilance including
Huntington's disease
Harness Therapeutics Advances First‑in‑Class Huntington’s Disease Candidate HRN001 and Forms Expert Clinical Advisory Board
As reported on PharmaBiz, Harness Therapeutics has selected HRN001 as its lead therapeutic candidate for Huntington’s disease (HD), marking a major milestone for the company
Rare Disease
Life Impact of Pain – Pain Series Part 2 of 3
Click here to see Part 1 of of this 3 part pain series. If you suffer with chronic pain, you not only live with the unrelenting
Obesity
Monthly Obesity Treatment Gets Easier: Lilly’s New Zepbound Pen Simplifies Weight Loss Injections
Patients using Zepbound for weight management now have a simpler option for administering their medication. As reported by PharmaLive.com, Eli Lilly received FDA clearance for
Prostate Cancer
Redefining Cancer Treatment: Podcast Interview with Dr. Charles Link on Sync-T and the Future of Immunotherapy
On this episode of Wait, How Do You Spell That?, host Bree Clare sits down with Dr. Charles Link, a pioneering oncologist whose career has
Bladder cancer
“At 44, I Thought I Was Starting Over” – Kristian’s Bladder Cancer Story
At 44 years old, I was ready to hit the reset button. In March of 2025, my partner and I stepped away from our careers.
Ovarian Cancer
British Columbia Researchers Develop a System to Reduce Ovarian Cancer by 80%
Ovarian cancer is a serious gynecological cancer with no reliable screening test, resulting in limited treatment options and a low number of survivors. Each year
Fibrodysplasia Ossificans Progressiva (FOP)
Breakthrough in Rare Bone Disease: FDA Fast-Tracks Garetosmab for Fibrodysplasia Ossificans Progressiva
Regeneron Pharmaceuticals announced that the U.S. Food and Drug Administration has accepted for Priority Review the Biologics License Application (BLA) for garetosmab, marking a significant
Datroway Receives U.S. Priority Review for First‑Line Treatment of Metastatic Triple‑Negative Breast Cancer
AstraZeneca and Daiichi Sankyo’s antibody‑drug conjugate Datroway (datopotamab deruxtecan) has been granted Priority Review by the U.S. Food and Drug Administration (FDA) for use as
Urea cycle disorders
More Than a Diagnosis: Gabriela’s Journey With Lysinuric Protein Intolerance, Urea Cycle Disorder, and Unshakable Faith
As a little girl, I believed miracles only existed in movies. They felt distant, beautiful stories meant for someone else. I never imagined that my
Psoriasis
Dual Approach to Disease: Eli Lilly’s Zepbound-Taltz Combination Demonstrates Breakthrough Results in Psoriasis Treatment
Eli Lilly is making strategic moves to expand its obesity medication Zepbound beyond weight management, demonstrating promising results when combined with its autoimmune therapeutic Taltz
Limb-girdle muscular dystrophy type 2A
My Journey with Limb-Girdle Muscular Dystrophy (LGMDR1)
Editor’s Note: This story was submitted to Patient Worthy by Ghulam Ali, Founder & CEO, Muscular Dystrophy Pakistan. I am 35 years old and hold
Cancer
Eat the Rainbow Winter Week 11: Satisfying Snacks
Editor’s Note: This article was shared with us by our friends at cancerdietitian.com. EtR PROGRAM UPDATES: Welcome to Week 11 of the Eat the Rainbow Fruit
Cancer
Triple-Target Immunotherapy for Solid Tumors Advances – Novel Antibody Enters Pivotal Testing Phase
A Chinese biopharmaceutical company has cleared a major regulatory milestone with a groundbreaking approach to cancer immunotherapy. As reported by PharmaBiz.com, the FDA has authorized
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Getting a diagnosis for Huntington’s disease is rarely simple. It often involves a combination of neurological exams, medical history, genetic testing, and imaging to help doctors understand what’s happening in the brain.
For many families, the process can bring a mix of answers, uncertainty, and difficult decisions—especially when genetic testing is involved. Learning about diagnosis and testing is an important step toward understanding the condition, accessing care, and supporting those affected.
Awareness helps ensure people recognize the signs, seek appropriate evaluation, and receive the support they deserve. If you're interested in sharing your story, click here: bit.ly/4dV7gru
#HuntingtonsDisease #HuntingtonsDiseaseAwareness #ShareYourStory #PatientWorthy
March is Brain Injury Awareness Month. Today and every day, we stand with survivors, caregivers, and the countless individuals navigating life after a brain injury. You are seen, supported, and never alone 💚 #braininjury #BrainInjuryAwarenessMonth #MoreThanMyBrainInjury #brainhealth
Patient Worthy is thrilled to share this video from Prxtrialport!
"Each story is different, but the message is collective: we walk different roads, yet we walk together. Every patient’s health journey is shaped by personal experience, cultural context, and healthcare systems, yet beneath those differences lie common threads that unite us."
#ClinicalTrials #RareDisease #PatientWorthy
