As reported on BioSpace, the FDA has extended its review of Novo’s investigational hemophilia A therapy denecimig due to manufacturing-related concerns, although the company says
As reported on Inside Precision Medicine, researchers at Stanford Medicine and the VA Palo Alto Health Care System have created a new urine test called
Editor’s Note: The following story was submitted to us by Pam Mason, Patient Speaker & Advocate. If you looked at a picture of me, you
I’ve survived Stage 4 colon cancer for about 10 years. I went to the doctor for a routine colonoscopy. They said I had a long
As reported on Medical Daily, small exploratory analysis suggests that semaglutide, the active ingredient in Wegovy, may substantially reduce liver fat in some adults with
When I was seven, my parents were trying to understand why I was becoming ill. I spent time in hospitals and underwent painful muscle biopsies.
Editor’s Note: Patient Worthy is honored to present this story, shared with us by our friends at the Courageous Parents Network. Originally written by Dr.
As reported on Becker’s Hospital Review, the FDA has approved a first-of-its-kind pulmonary heart valve that can be enlarged after implantation, potentially allowing the device
As reported on Becker’s Hospital Review, an FDA advisory committee has backed Grail’s Galleri blood test, bringing the U.S. closer to potentially having its first
Editor’s Note: Patient Worthy is honored to share this article from our friend Julie Lanford, MPH, RD, CSO, LDN – a.k.a. The Cancer Dietitian. To
Editor’s Note: Patient Worthy is honored to share the following story from our friends at Elephants & Tea, originally written by Michelle Lawrence, a patient
As reported on SciTechDaily, a large research review suggests age-related losses in muscle mass, strength, and physical function may have a stronger association with dementia
Investigational once-monthly therapy significantly reduced proteinuria versus placebo at 37 weeks, according to interim findings from the phase 3 study. As reported on PharmaBiz, Roche
Editor’s Note: Patient Worthy is proud to share the following story from our friends at Elephants & Tea, originally written by Dillon Groover, a brain
Editor’s Note: Patient Worthy is honored to share this article from our friends at Rareative. To see the article in its original format, please click
As reported on PharmaBiz, the FDA has accepted AstraZeneca’s supplemental Biologics License Application for durvalumab plus neoadjuvant enfortumab vedotin in patients with muscle-invasive bladder cancer
As reported on ONC Live, early findings from the phase 1/2 RALLY-MF trial suggest selcodebart may improve hemoglobin levels and reduce dependence on red blood
Once concentrated largely in tropical and subtropical regions, dengue is posing an expanding public health challenge as climate conditions, urbanization and population movement increase the
Project Alive #HunterSyndromeHunter Syndrome Awareness Week is coming!
The third week of October is our opportunity to come together, raise our voices, and help more people learn about Hunter syndrome (MPS II). Whether you are a parent, sibling, family member, friend, or supporter, there are so many ways to get involved.
👕 Wear your support! Order your Hunter Syndrome Awareness Week “Fighting for Their Future” T-shirt and help spread awareness wherever you go.
store.projectalive.org/
📣 Bring Awareness Week to your community! Ask your local city, county, or state representatives to officially recognize Hunter Syndrome Awareness Week. We’ve created sample letters and a resolution template to make it easy to get started.
projectalive.org/advocacy#HSAW
Let’s make Hunter Syndrome Awareness Week impossible to miss.
#HunterSyndromeAwarenessWeek #HunterSyndrome #ProjectAlive #MPSII #FightingForTheirFuture
International Rett Syndrome FoundationDue to technical difficulties, IRSF's Rett in Focus Webinar, When Research Can't Answer Every Question, has been rescheduled for next Wednesday, October 14, at 3 p.m. ET. Join IRSF's Chief Scientific and Medical Officer, Dr. Dominique Pichard, and guest speaker Erin O'Connor Prange, MSN, CRNP, from CHOP, for this 30-minute conversation offering insight into how expert consensus may help shape care in Rett syndrome when research alone does not provide clear guidance.
Register today and submit your questions for the speakers: us02web.zoom.us/webinar/register/WN_3Lr3lRYUTxSdsOSIvSEaeg
This webinar is presented in partnership with Acadia Pharmaceuticals.
© Copyright 2024 Patient Worthy
Sign Up With a Patient Worthy Account and Share Your Rare Story
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
