The Basic Problem: Why One Bad Gene Can Cause Big Trouble Imagine your body as a giant factory. Like any factory, it needs quality control—machines
As reported on BioSpace, the U.S. Food and Drug Administration has approved Regeneron’s Pasatru (garetosmab) for adults with fibrodysplasia ossificans progressiva (FOP), a rare genetic
Historic Milestone Offers Relief from Relentless Burden of Glycogen Storage Disease Type Ia According to a recent press release from Ultragenyx, after decades of medical
As reported by allsci, China’s National Medical Products Administration (NMPA) has granted conditional approval to TransThera Sciences’ Yochanra (tinengotinib) for adults with unresectable, advanced, or
As reported by PharmaBiz, Zydus Lifesciences has announced the launch of Revahale (revefenacin), a once-daily nebulized long-acting muscarinic antagonist (LAMA) for the maintenance treatment of
What Happened? Hansa Biopharma, a Swedish company, announced that the first patient in Australia has successfully received a kidney transplant after being treated with a
As reported on BioSpace, AstraZeneca has discontinued a pivotal Phase 3 trial evaluating its investigational bispecific antibody volrustomig in advanced non-small cell lung cancer (NSCLC)
New observational research suggests that addressing obesity alongside inflammatory joint disease could improve treatment outcomes for people with psoriatic arthritis (PsA). As reported on MedIndia,
As reported on News Medical, researchers are highlighting a new class of therapies that could improve outcomes for people living with primary biliary cholangitis (PBC),
Researchers at MIT have identified a potential new approach to reducing lung cancer risk by targeting caspase-1, an enzyme involved in inflammation. Findings published in
A recent study shared by The Lancet shows that a first-in-class investigational therapy targeting neurotrophin-3 (NT-3) significantly reduced pain and improved function in patients with
As reported by the ICIJ, the FDA originally approved Keytruda (pembrolizumab) combined with cisplatin and gemcitabine on October 31, 2023, to treat locally advanced inoperable
Editor’s Note: Patient Worthy is honored to present this article, originally written by Camille Johnson. People living with chronic illness or long-term treatment plans often
Editor’s Note: Patient Worthy is honored to share this article with you, kindly provided to us by our friends at End Sepsis. To see the
If you had asked me a few years ago what I thought my biggest health concern would be, lung cancer wouldn’t have even crossed my
Reflections on V122I, Genetic Risk, and the Questions Black Families Are Still Asking Editor’s Note: This article was written and submitted to us by Erin
According to recent reports, assistant pediatric professor at the Boston Children’s Hospital, Prof. Meenakshi Rao, noted that infections associated with Clostridioides difficile (C. Diff.) are difficult to eradicate. Nonetheless,
For more than 20 years, I had a treatment routine that worked. My specialty pharmacy delivered the medications I needed and coordinated trained nurses who
Pruritus can be more than an occasional itch. When persistent or severe, it can interfere with sleep, concentration, comfort, and everyday activities. It may be associated with skin conditions, medications, or underlying systemic, neurological, and rare diseases. Raising awareness of symptoms like pruritus helps highlight how something that may seem minor can have a significant impact on quality of life.
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Your experience may be exactly what someone else in our community needs to read today. 🌻
#PatientWorthy #raredisease #chronicillness #PatientVoice #shareyourstory #RareDiseaseCommunity #chronicillnesscommunity
Progress doesn’t always come with a big milestone or something others can see. Sometimes, it’s knowing your body better, asking the questions you once hesitated to ask, finding what works for you, or realizing you’re handling hard days differently than you used to. 🤍 Give yourself credit for the progress that happens quietly—it still counts. #ProgressNotPerfection #HealthAwareness #PatientWorthy
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