Welcome to Study of the Week from Patient Worthy. In this segment, we select a study we posted about from the previous week that we
Compassion [kuhm–pash-uhn] noun A feeling of deep sympathy and sorrow for another who is stricken by misfortune, accompanied by a strong desire to alleviate the
Welcome to the Rare Classroom, a new series from Patient Worthy. Rare Classroom is designed for the curious reader who wants to get informed on
Welcome to the Rare Classroom, a new series from Patient Worthy. Rare Classroom is designed for the curious reader who wants to get informed on
Regeneron Pharmaceuticals has recently announced the results of Phase 2 of their study of pozelimab, which is an experimental treatment for paroxysmal nocturnal hemoglobinuria.
“I’ll be honest with you, Lindsey. I had to look up your syndrome before this appointment,” the doctor bashfully admitted. “I have never seen or
On August 2, 2021, biotechnology company Amicus Therapeutics (“Amicus”) shared that its oral treatment Galafold (migalastat) was approved by the European Commission (EC) for the
A new study published in the journal Scientific Reports has helped explain the differences between neuromyelitis optics spectrum disorder (NMOSD) after optic neuritis (ON) and multiple sclerosis
According to a press release from late July 2021, LX1004, a treatment for patients with CLN2 Batten disease, received both Orphan Drug and Rare
Clinical guidelines are often used to improve patient treatment. These guidelines use evidence reviews, as well as an examination of other standards-of-care, to optimize
In the past, researchers have questioned whether an association exists between Lyme disease and psychiatric or mood disorders such as depression, anxiety, or even suicidal
Huafrid Billimoria is a 25-year-old triathlete in India. He has just become the first person diagnosed with cervical dystonia in the country to complete a
Welcome to Study of the Week from Patient Worthy. In this segment, we select a study we posted about from the previous week that we
As of today, the world has been battling the COVID-19 pandemic for over 1.5 years. Throughout the world, the novel coronavirus is responsible for 197
A recent study has examined what risk factors exist for patients diagnosed with myotonic dystrophy, the most common of all muscular dystrophies. This is a
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