As reported on MedCity News, Eli Lilly has reported encouraging early-stage clinical data for AJ1-11095, an investigational therapy for myelofibrosis acquired through its recent purchase
My name is Les Howard, and I am living with hypertrophic obstructive cardiomyopathy (HCM). Looking back, I believe I may have lived with HCM for most
As reported on PharmaBiz, Sumitomo Pharma America (SMPA) presented new clinical and translational data spanning myelofibrosis (MF) and acute leukemia programs at the 2026 European
In the United States, colorectal cancer represents the third most frequently diagnosed malignancy and the second leading cause of cancer-related death. A colonoscopy continues to
Grifols, as announced in a recent press release, has officially launched FESILTY™ (fibrinogen, human-chmt) in the United States. The therapy is approved to treat sudden,
As reported by the BBC, landmark advance in type 1 diabetes care has been reached with the introduction of teplizumab, the first treatment shown to
Further to the WHO’s official confirmation of an outbreak of 300 Ebola cases as of May 2026, health authorities in the Democratic Republic of the
Every single day, the average person inhales thousands of microscopic fungal spores. For most of us, our immune systems destroy these tiny invaders before they
As reported on Scientific American, a growing body of research suggests that Alzheimer’s disease progression is driven by a complex interplay between beta-amyloid plaques and
Editor’s Note: This story is a continuation of Jenny Decker’s global sailing voyage. To see the original article, please click here. Jenny Decker left Hawaii in
Recently at the World Orphan Drug Conference in Boston, Patient Worthy had the opportunity to meet with Dave Pearce PhD, Chair of International Rare Disease
As reported on Yahoo News, a combination therapy involving nivolumab (Opdivo) from Bristol Myers Squibb and cabozantinib (Cabometyx) from Exelixis has demonstrated substantial clinical benefit
Editor’s Note: This article was shared with us by our friends at the Courageous Parents Network. To see the article in its original format, please
In a recent statement, CONNECTA Therapeutics, a biotechnology company focused on disorders of the central nervous system, has announced the start of its Phase IIa
As seen in the CDC’s recent reports, 0.6 per 100,000 people were hospitalized in mid-April with confirmed hospital admissions averaging between 800 to 900 in
As reported on Medscape, global phase 3 clinical trial suggests that veligrotug, an investigational monoclonal antibody targeting the insulin-like growth factor‑1 receptor (IGF‑1R), may offer
As reported on Becker’s Hospital Review, the U.S. Food and Drug Administration (FDA) has issued updated guidance targeting how telehealth companies promote compounded medications, particularly
As reported on CNET, parents and caregivers now have a new option to help monitor children’s blood sugar levels at home. The US Food and
💙 Pain may be part of the journey, but it doesn't have to define the story.
Struggles can become strength. Challenges can inspire courage. And battles fought in silence can give hope to someone who needs it most.
✨ Every obstacle overcome has the power to make a difference in someone else's life.
#StrongerTogether #PatientWorthy #resilience #chronicillnesswarrior #patientadvocate #inspiration #RareDiseaseCommunity #youarenotalone #keepgoing
Sometimes the things that take the most effort are the things nobody else sees.
Making the appointment. Asking the question. Speaking up when something doesn't feel right. Resting before you hit a wall. Keeping up with medications, paperwork, and everything in between.
They may seem small from the outside, but they can take a lot of energy.
If you've done any of these lately, give yourself credit. Those small wins matter more than you think.
#chronicillness #invisibleillness #raredisease #youarenotalone #PatientWorthy
THE WOBBLES
It’s one of the first things many people notice about children with Ataxia-Telangiectasia
They sway when they stand. They stumble when they walk. They wiggle. They shift. They move constantly.
Charlotte’s “wobbles” are part of her daily life and some days they’re more noticeable than others. What many people don’t realize is that for children with A-T, staying still can be incredibly difficult. It’s exhausting for them. Their brains are constantly working to coordinate movements that most of us never have to think about. Even something as simple as standing in one place, sitting upright, or waiting for your turn during swim lessons takes incredible effort.
# Ataxia-Telangiectasia #charlottesstory #charlottescure #ataxiatelangiectasia #atchildrensproject #PatientWorthy #StoryShare
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