HIV/AIDS
FDA Reviews Gilead’s Once-Weekly Oral Lenacapavir for HIV Prevention
As reported on Business Wire, Gilead Sciences has announced that the U.S. Food and Drug Administration (FDA) has accepted its supplemental New Drug Application for
FDA Clarifies Marketing Limits for Compounded GLP-1 Drugs Amid Ongoing Enforcement Effort
- June 20, 2026
FDA Clears First Over-the-Counter Continuous Glucose Monitor for Children
FDA Approves Pembrolizumab–Belzutifan Combination for Adjuvant Treatment of High-Risk Clear Cell RCC
FDA’s New Framework Signals Turning Point for Rare Disease Therapies—But Major Barriers Remain
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Lynch syndrome
Hereditary Cancer Risk Is Harder to Detect When Family History Crosses Borders
I grew up believing health was something you could control if you were disciplined enough. In my Chinese immigrant family, my father talked constantly about
Diabetes Type 1
FDA Grants Accelerated Approval to Teplizumab for Newly Diagnosed Pediatric Type 1 Diabetes
As shared in a recent press release, the U.S. Food and Drug Administration (FDA) has granted accelerated approval to teplizumab (Tzield) for a new pediatric
Idiopathic Hypersomnia
Alkermes’ Alixorexton Gains Orphan Drug Status in the US and EU
As reported by Pharmaceutical Technology, Alkermes has announced that its investigational therapy alixorexton has received orphan drug designation from both US and European regulators, marking
IgA Nephropathy
AstraZeneca’s Ravulizumab Receives FDA Priority Review for IgA Nephropathy
As reported on PharmaBiz, AstraZeneca has announced that the US Food and Drug Administration (FDA) has accepted for review a supplemental Biologics License Application (sBLA)
Rare Disease
FDA Signals Shift Toward Bayesian Methods in Clinical Trials
As reported on MedCity News, the U.S. Food and Drug Administration (FDA) has issued draft guidance encouraging the thoughtful use of Bayesian statistical approaches in
Thyroid eye disease
Glycemic Monitoring Recommended for All Patients Receiving Teprotumumab in Thyroid Eye Disease
Emerging evidence, as reported by the American Academy of Ophthalmology, suggests that glycemic surveillance should be considered for all patients undergoing teprotumumab therapy for thyroid
Rare Disease
Aortic Valvotomy, A Widening of Heart Valves
When Seth Wharton was only one month old, doctors repaired his narrow heart valve. Then, five years later, he was referred to UAB Cardiovascular Institute
Dravet Syndrome
An Update from the Dravet Syndrome Foundation
Madrid, June 5th, 2026 The Dravet Syndrome Foundation received the Merck Innovation Talent Award for a scientific publication regarding a tool that assesses neuropsychiatric issues
Neurotrophic Keratopathy
TearSolutions Advances Lacripep® for Neurotrophic Keratitis with FDA Designations and Phase 2 Trial Launch
As reported on Business Wire, TearSolutions, a clinical-stage biotechnology company focused on ophthalmic therapies, has announced key regulatory and clinical progress for its investigational drug
Fabry Disease
Fabry International Network’s Young Adult Guidebook
Website: https://fabrynetwork.org/youngadults Instagram Young Adults: @fabryyoungadults Instagram FIN: @fabryintnetwork 11 June 2026 – FIN launches international Young Adults Guidebook created by and for young adults
Parkinson's Disease
Finding Balance: David and Charice’s Journey with Parkinson’s Disease
When David Williams noticed a slight tremor in his right hand, he convinced himself it was something manageable, perhaps a compressed nerve that would eventually
Rare Disease
FDA Clears New Sunscreen Ingredient After Two-Decade Gap
In a notable update for dermatologic and consumer health, the U.S. Food and Drug Administration (FDA) released a press statement disclosing their authorization of the
Cancer
FDA’s Real-Time Clinical Trial Model: Transforming Oncology Care While Raising New Challenges
As reported on Becker’s Hospital Review, the U.S. Food and Drug Administration’s launch of a real-time clinical trial model marks a notable shift in how
Cancer
Onchilles Pharma Initiates First-in-Human Trial of N17350 for Advanced Solid Tumors
As reported on Business Wire, Onchilles Pharma has announced the first patient dosing in a Phase 1/2 clinical trial evaluating its investigational therapy, N17350, in
Diabetes Type 2
Eli Lilly Advances Oral GLP‑1 With Strong Phase 3 Data in Type 2 Diabetes
As reported on BioSpace, Eli Lilly is moving closer to expanding the use of its oral GLP‑1 receptor agonist orforglipron, marketed as Foundayo, into type
Rare Disease
Omnix Medical Advances OMN6 Into Phase II Trial for Drug-Resistant Acinetobacter Infections
As reported on PharmaBiz, Omnix Medical has reached a key clinical milestone with the initiation of patient dosing in a phase II study of its
Pancreatic Cancer
Early Clinical Trial Suggests Promise for New Pancreatic Cancer Drug Combination
As reported on STAT News, a novel combination of investigational therapies from Tango Therapeutics and Revolution Medicines is generating cautious optimism after demonstrating notable tumor
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Thyroid Eye Disease can change how you see the world and how the world sees you. Because symptoms can develop gradually or be mistaken for something else, many people don’t realize what’s happening right away.
That’s why awareness and testing are so important. A diagnosis is more than a label. It’s a step toward understanding your symptoms, finding the right care, and protecting your vision for the future. If something feels different with your eyes, it deserves attention. The sooner you have answers, the sooner you can take control of your health. Visit patientworthy.com for more information on TED.
#ThyroidEyeDisease #TEDAwareness #EyeHealth #EarlyDetection #PatientWorthy
Some weeks feel heavier than others.
In those moments, it’s often not the big things that make the difference—it’s the small acts of understanding. A doctor who listens. Clear answers. Flexible plans. A message checking in. Someone asking how you're really doing.
What’s one small thing that can make a hard week feel a little lighter for you?
#ChronicIllness #InvisibleIllness #RareDisease #PatientWorthy
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