Colorectal cancer
When the Silence Got Loud
Editor’s Note: Patient Worthy is honored to share this story from our friends at Elephants & Tea, originally written by Bill Phillips, a colorectal cancer
Dual-Drug Strategy Shows Promise Against Treatment-Resistant Prostate Cancer
- September 9, 2026
BMS Achieves Milestone with Next-Generation CAR-T Therapy for Multiply-Treated Myeloma Patients
To Stand Beside Suffering
Machine Learning Maps and Discovers Clinical Endpoints in Pompe Disease Using Real-World Data
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PTEN Hamartoma Tumor Syndrome
New PTEN Research Could Help Predict Cancer Risk in Rare Genetic Syndrome
A single genetic change can have dramatically different effects from one person to the next. That is the reality for people living with PTEN hamartoma
Diabetes Type 2
FDA Expands Mounjaro’s Label to Include Cardiovascular Risk Reduction in Type 2 Diabetes
As reported on QZ, the U.S. Food and Drug Administration has approved a new indication for Eli Lilly’s tirzepatide (Mounjaro), allowing the therapy to be
Polycythemia vera
FDA Clears Takeda’s Mimrylo for Polycythemia Vera, Introducing a Novel Treatment Option
As reported on MedCity News, the U.S. Food and Drug Administration has approved Takeda Pharmaceutical’s Mimrylo (rusfertide) for the treatment of erythrocytosis in adults with
Colorectal cancer
BioNTech Ends Phase 2 Trial of Personalized mRNA Therapy in High-Risk Colorectal Cancer
As reported on Drugs, BioNTech has decided to halt development of its Phase 2 BNT122-01 study investigating autogene cevumeran (BNT122/RO7198457) in patients with resected colorectal
Gastroesophageal junction carcinoma
Phase 3 HERIZON-GEA-01 Analysis Strengthens Survival Evidence for Zanidatamab-Based Regimens in HER2-Positive Gastroesophageal Cancer
As reported on PharmaBiz, BeOne Medicines has reported positive results from the second interim analysis of the phase 3 HERIZON-GEA-01 trial, further supporting the use
Leukemia
Think Beyond Remission to Protect the Life We Saved: A Young Man’s Journey with T-cell Acute Lymphoblastic Leukemia/Lymphoma
At 22, a young person’s world should be filled with possibilities—a career to build, places to travel, friendships to make, and a future to imagine.
Essential thrombocytosis
FDA Approves PharmaEssentia’s Besremi for Essential Thrombocythaemia
As reported on Pharmaceutical Technology, the US Food and Drug Administration (FDA) has granted approval to PharmaEssentia’s Besremi (ropeginterferon alfa-2b-njft) for the treatment of adults
Multiple Sclerosis
Novartis’ Remibrutinib Cuts Relapse Rates in Phase III Multiple Sclerosis Studies
In a recent press release, Novartis has reported positive topline results from its Phase III REMODEL-1 and REMODEL-2 trials, showing that the investigational oral Bruton’s
Metastatic Breast Cancer
EU Approves Enhertu Plus Pertuzumab for First-Line HER2-Positive Metastatic Breast Cancer
As reported on Business Wire, the European Commission has approved trastuzumab deruxtecan (Enhertu) in combination with pertuzumab for the first-line treatment of adults with unresectable
Rare Disease
Novartis Suspends Eight CAR-T Studies After Patient Deaths Trigger Safety Review
As reported in the European Medical Journal, Novartis has paused eight clinical studies evaluating its experimental CAR-T cell therapy, known as rap-cell, after three trial
Neurofibromatosis Type 1
Cherry Angiomas May Represent an Underrecognised Vascular Feature of Neurofibromatosis Type 1
As reported in the European Medical Journal, new research suggests that cherry angiomas occur more frequently and at an earlier age in people with neurofibromatosis
Hereditary angioedema
BioCryst Wins Japanese Approval for Pediatric Use of ORLADEYO in Hereditary Angioedema
In a recent press release, BioCryst Pharmaceuticals has shared that it received approval from Japan’s Ministry of Health, Labour and Welfare for the use of
Oral cancer
New Brush Test Could Make Oral Cancer Detection Easier
As reported on Inside Precision Medicine, a new, non-invasive test may help doctors detect oral cancer quickly and reduce the need for painful scalpel biopsies.
Rare Disease
You Do Not Need to Be Healed to Be Held: Love and Chronic Illness
Have you ever looked in the mirror and wondered, “Who am I now? Why did this diagnosis happen to me? When will this be over?
Dermatomyositis
Roivant and Priovant Secure FDA Approval for First Targeted Oral Therapy for Dermatomyositis
As reported on Pharma Phorum, Roivant Sciences and its subsidiary Priovant Therapeutics have received U.S. Food and Drug Administration (FDA) approval for Lisraya (brepocitinib), marking
non-small cell lung cancer
AstraZeneca Secures Global Rights to EGFR-Targeted Lung Cancer Therapy ZEGFROVY
As reported on Business Wire, AstraZeneca has finalized its previously announced licensing agreement with Dizal Pharmaceutical, gaining exclusive worldwide rights to develop and market ZEGFROVY
Rare Disease
Basking Biosciences formulates Reversable Clot Busting Therapy for Acute Stroke
Treating acute ischemic strokes involves a precarious clinical balance: physicians must dissolve arterial clots to save brain tissue without triggering catastrophic intracranial hemorrhaging. To address
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If my search history could talk...
It would tell the story of questions.
The first search for a symptom that didn't feel quite right. The medical term you had to look up three times before you could pronounce it. The test result that led to more questions than answers. The diagnosis you'd never heard of until it suddenly became part of your life.
It would remember the late-night searches, the moments of uncertainty, and the endless scrolling for someone, anyone, with a similar experience.
Because behind every search is something deeply human: curiosity, confusion, fear, learning, and the desire to understand.
Sometimes the journey starts with a question. Sometimes it starts with a hundred.
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Awareness starts with understanding.
Multiple myeloma can be complex, and learning more about the condition is an important step toward greater recognition, education, and support for those impacted.
Swipe through for a quick overview, and help us spread awareness by sharing this post with your community. If you're interested in sharing your story with multiple myeloma, click here: ow.ly/tWzH50ZKYUj or the link in our bio!
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