Rare Disease
Regular Yoga Practice Improves Cardiometabolic Health
Yoga is often celebrated for its ability to help people find their “zen,” but new research shows it might be doing some heavy lifting for
Motif Neurotech Gains FDA Clearance to Launch First-in-Human Trial of Implantable BCI for Depression
- April 28, 2026How to Transform Your Skin with Simple Natural Care Habits
Breakthrough in Pancreatic Cancer Treatment: How Revolution Medicines’ RAS Inhibitor Is Reshaping Patient Outcomes
Ultomiris Reduces Proteinuria in Phase III Trial for IgA Nephropathy
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Parkinson's Disease
AskBio Scales Up Gene Therapy Manufacturing for Landmark Parkinson’s Disease Trial
AskBio Inc., a gene therapy subsidiary of pharmaceutical giant Bayer AG, has taken a significant step forward in advancing treatment options for Parkinson’s disease. According
Moebius Syndrome
Awareness Isn’t the Hard Part — What 18 Years in the Moebius Syndrome Community Has Taught Me
For nearly two decades, I’ve been building and maintaining a global online community for individuals and families affected by Moebius syndrome, a rare neurological condition
Multiple Sclerosis
From Overlooked to Unstoppable: The Mendoza Story That Inspired a Nation
Fernando Mendoza’s journey to becoming the Las Vegas Raiders’ first overall NFL Draft pick is not a typical underdog narrative, it’s a testament to resilience,
Breast Cancer
Choosing Hope
Editor’s Note: Patient Worthy is honored to share this piece from our friends at Elephants & Tea, originally written by Katie Newbaum. To see the
Rare Disease
Ophthalmologist Emerges as Leading Candidate to Head FDA Vaccine Division
As reported on NBC News, an ophthalmologist with a history of criticizing the U.S. government’s Covid-19 vaccine strategy is emerging as a leading contender to
Glioblastoma
Maha & Baba: A Caregiver’s Journey Through Glioblastoma
My name is Maha, and I had the privilege of being my father’s — my Baba’s — caregiver. I’ll be blunt; it was tough. When
Psoriasis
One-Year Data Reinforces Icotyde’s Position as Transformative Psoriasis Therapy: Sustained Clearance and Favorable Safety Profile
Johnson & Johnson announced promising long-term efficacy and safety data for Icotyde (icotrokinra), the first and only targeted oral peptide that precisely blocks the IL-23
Multiple Sclerosis
Roche’s Elecsys NfL Blood Test Gains CE Mark for Monitoring Neuroinflammation in MS
As reported on PharmaBiz, Roche has secured CE mark approval for its Elecsys Neurofilament Light Chain (NfL) assay, a blood-based test designed to help detect
Brain Cancer
Invading the Blood Brain Barrier: FDA Approves Pembrolizumab Combo
Astrocytoma and glioblastoma are fast-growing brain cancers that often return after surgery, with survival for astrocytoma patients averaging only four to five months. While medications
Atopic dermatitis
Lynk Pharmaceuticals Achieves Regulatory Milestone: Zemprocitinib Advances in China for Atopic Dermatitis Treatment
Lynk Pharmaceuticals announced a significant development in its pipeline with the China National Medical Products Administration (NMPA) formally accepting the New Drug Application (NDA) for
Cervical Dystonia
5 Lessons Nature Taught Me About Living with Pain and Dystonia
I’ve always been a nature lover. I like nothing better than going for a hike in the woods or strolling along the beach or gazing
Lymphoma
What We Carry With Us: The Lesson of the Quilt
Editor’s Note: Patient Worthy is honored to share this submission by Regina Portnoy, a clinical researcher with 20 years of experience working alongside patients. Many
Small cell lung cancer
Breakthrough Lung Cancer Therapy Advances: Ifinatamab Deruxtecan Receives FDA Priority Review for Small Cell Lung Cancer
Daiichi Sankyo and Merck announced a significant regulatory milestone with the FDA’s acceptance and Priority Review of ifinatamab deruxtecan (I-DXd), a potentially first-in-class therapeutic targeting
Duchenne Muscular Dystrophy
Roche to Launch New Elevidys Trial After European Rejection — What’s Going On?
As reported on BioPharmaDive, Roche is restarting efforts to get Elevidys, a gene therapy for Duchenne muscular dystrophy (DMD), approved in Europe by launching a
Breast Cancer
Katrina’s Journey with Metastatic Breast Cancer
I’ve always been an overachiever – someone who puts their mind to something and delivers more than was expected, someone who strives for greatness. I
Uveal melanoma
Darovasertib-Crizotinib Combination Achieves Breakthrough Efficacy in Metastatic Eye Cancer
IDEAYA Biosciences and Servier announced promising Phase 2/3 trial results for darovasertib, a selective PKC inhibitor, combined with crizotinib in the treatment of metastatic uveal
HIV/AIDS
Norway Case Adds Insight Into Long-Term HIV Remission After Stem Cell Transplant
As reported on Healthline, a man in Norway has entered sustained HIV remission following a stem cell transplant, becoming one of a small number of
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Aplastic anemia is a rare condition that affects how the body makes blood cells. Because it impacts red blood cells, white blood cells, and platelets, it can affect everything from energy levels to the body’s ability to fight infections and stop bleeding.
Raising awareness helps people better understand this rare blood disorder and the challenges those affected may face.
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