Osteosarcoma is a diagnosis no family should ever have to face. It is the most common primary bone cancer in children and adolescents, yet treatment
A groundbreaking genetic study published in The Journal of Clinical Endocrinology & Metabolism and reported by ScienceDaily.com has revealed that obesity and high blood pressure
Twenty years is a long time to believe a cancer chapter has closed. For two decades after my radical prostatectomy, I lived with the quiet
Editor’s Note: Patient Worthy is honored to share part 1 in an ongoing 10-part series, written and shared with us by Elena Genik. When Everything
A growing body of research shows that sleep quality, dietary sodium, and hypertension are more closely linked than once believed — and two major healthcare
Vera Therapeutics announced a major milestone in drug development on January 7, 2026, when the U.S. Food and Drug Administration granted Priority Review to the
As reported by the European Pharmacy Review, a combination approach using Johnson & Johnson’s small‑molecule therapy Caplyta (lumateperone) alongside standard antidepressants continues to show promising
A newly published Phase 1/2 study in The New England Journal of Medicine, and reported on by the Manila Times, highlights promising early results for tividenofusp
A New Approach to a Persistent Problem Celcuity has reached a critical inflection point in its pursuit of a novel breast cancer treatment. The FDA’s
As reported on Healio, glucagon-like peptide-1 (GLP-1)–based therapies are rapidly reshaping the landscape of diabetes and chronic kidney disease (CKD) management. Originally developed for glycemic
Immunoglobulin A nephropathy (IgAN) remains one of the most common primary glomerular diseases worldwide, yet effective treatments are limited. A new study, recently published in
If you got past the title without rolling your eyes or getting angry (I understand if you did either or both as you will see
Breaking the Cycle of Prescription Dependency The opioid epidemic that has devastated American communities for decades may finally have a novel challenger. According to Bezinga.com,
As reported by Clinical Trials Arena, Axsome Therapeutics has begun dosing patients in its FORWARD Phase III clinical trial, a pivotal study designed to evaluate
Brussels — On February 24, 2026, the acclaimed Netflix documentary The Remarkable Life of Ibelin received the Media & Awareness Raising Award at the EURORDIS
The Three-Year Fight That Changed Everything When Giles Turner learned his postcode could determine whether he received life-saving cancer treatment, he didn’t accept it quietly.
As reported on PM Live, a new clinical trial hub focused on epidermolysis bullosa (EB) has been established at University Medical Center Groningen (UMCG) in
To the patient, the parent, the caregiver, and the person in the “limbo” of waiting: I am one of you. My name is Aaron Jackson,
Cambridge Rare Disease NetworkWe’ll be joining the global chorus of voices to highlight that, although individually rare, having a rare or undiagnosed condition is actually very common, yet our community so often remains unseen and unsupported.
There are various ways you can get involved with Rare Disease Day throughout the month:
#LivingRARE - Join us for our in person event in Cambridge for Rare Disease Day camrarerarediseaseday2026.eventbrite.co.uk/
#LightUpForRare - Around the world at 7pm local time on 28th Feb people will be lighting up buildings, lighting or decorating their homes (or themselves!) to spread the word in a global chain of light!
#ShareYourColours - Share your own unique experiences.
Be #RareAware - If you don't want to share your own story, or don't have a direct connection to rare disease, you can still get involved by sharing facts and other people's stories by searching the #RareDiseaseDay hashtag, and help to spread the word about rare.
#ShowYourStripes - Join @medics4rarediseases and wear your stripes
Fun fact:
Why is Rare Disease Day the last day in February?
Because during a leap year the last day in February is the 29th - the rarest date in the calendar!
#datacollection Homocystinuria - HCU Network AmericaHave questions about RareX? We’ve got answers! 💬
Join our virtual open office hours this Thursday, February 4th, from 12–2 PM MST to connect with our Research Coordinator and learn how to navigate the Homocystinurias Data Collection Program.
Drop in anytime during the window—no pressure, just support. 💙
🔗https://bit.ly/RarexOfficeHours
#HCUHero #RareX #Podcast #Hope #International #Homocystinuria #newbornscreening #genetics #Classical #coblamindisorders #severeMTHFR #lowprotein #lowproteindiet #medicalformula #raredisease #research #advocacy #treatment #Connection
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