Biossil, based in Toronto and co-founded by Dr. Alexander Mosa (Chair, CSO and co-founder) and Anthony Mouchantaf (CEO and co-founder), is making headway for rare
As reported on PharmaTimes, Poolbeg Pharma has secured a Canadian patent protecting the use of p38 MAPK inhibitors, including its lead candidate POLB 001, for preventing
Editor’s Note: This story was originally published on Linked-In and is shared with permission by Olga Lucia Torres. She waited an hour and fifteen minutes to
As reported on Healio, emerging real-world evidence suggests that glucagon-like peptide-1 (GLP-1) receptor agonists—and related dual agonists—may play a significant role in lowering the risk
I remember the day I realized something was wrong, as clearly as if it happened this past weekend. It was a beautiful morning in June.
Systemic lupus erythematosus punishes patients twice. First comes the disease itself, an autoimmune disorder where the body attacks its own tissues, causing debilitating fatigue, joint
As reported on BioSpace, the U.S. Food and Drug Administration (FDA) has approved Partner Therapeutics’ bispecific antibody Bizengri for adults with cholangiocarcinoma harboring an NRG1
Editor’s Note: Patient Worthy is honored to share this submission from Katie DiLorenzo, SVP, Patient and Pharmacy Services, PANTHERx® Rare. If you’re living with a
Mesenchymal stromal cells (MSCs) have tantalized the medical world for years. These versatile immune-modulating cells offer genuine hope for diseases ranging from epidermolysis bullosa, a
Patient Worthy is honored to reprint this selection from The Cancer Dietitian, by Julie Lanford MPH, RD, CSO, LDN. It’s important to know that no single
I am sharing my journey to give a voice to patients who suffer from extreme poly-pathology and are often left behind by the medical system.
For decades, colorectal cancer treatment has followed the same playbook: surgeons remove the tumor, then patients endure months of chemotherapy hoping to catch any remaining
AskBio Inc., a gene therapy company operating independently under Bayer AG, has taken a key step forward in the development of its investigational Parkinson’s disease
Editor’s Note: This story was originally published on Linked-In and is shared with permission by Olga Lucia Torres. In college, a clinician told me I
Enpatoran offers hope for millions suffering from lupus skin manifestations Pharmaceutical company Merck KGaA has announced a significant milestone in lupus treatment research. As reported
As reported on PharmaBiz, Vanda Pharmaceuticals has launched a new clinical trial, known as Thetis, to evaluate whether its neurokinin‑1 (NK‑1) receptor antagonist Nereus (tradipitant)
Editor’s Note: Patient Worthy is honored to present this article, shared with us by our friends at the Seena Magowitz Foundation. When doctors diagnosed Michael
A major breakthrough for the 300 Irish patients living with butterfly skin. For the first time in Ireland, patients battling epidermolysis bullosa, a rare and
💙 Understanding Becker Muscular Dystrophy (BMD)
Becker Muscular Dystrophy is a genetic condition that leads to progressive muscle weakness, most often affecting the hips, thighs, and legs. Everyday activities like climbing stairs, running, or maintaining balance can become more difficult over time.
While BMD progresses more slowly than other forms of muscular dystrophy, it can also impact the heart and overall mobility. Early awareness, ongoing care, and support can make a meaningful difference in quality of life.
✨ Let’s raise awareness, support those affected, and continue advocating for research and better treatments.
If you'd like to share your story with us, click here: bit.ly/4dV7gru
#BeckerMuscularDystrophy #BMDawareness #MuscularDystrophy #ShareYourStory #PatientWorthy
For many people living with rare neurological or vestibular conditions, the world may appear to move or bounce even when standing still. Symptoms like this can affect balance, reading, walking, driving, and everyday activities in ways that are often invisible to others. Raising awareness helps bring attention to the complex ways rare diseases can affect vision and neurological function, and why understanding these experiences matters.
#rarewordoftheweek #raredisease #rarediseaseawareness #PatientWorthy
When Breakthrough Drugs Need a New Home: Inside the Arvinas-Rigel Partnership bit.ly/4nw4r59 Read now at PatientWorthy.com
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