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PATIENT WORTHY SERIES

Study of the Week: Hereditary Angioedema Could Increase Cancer Risk

Welcome to Study of the Week from Patient Worthy. In this segment, we select a study we posted about from the previous week that we

Rare Classroom: Uveitis

Welcome to the Rare Classroom, a new series from Patient Worthy. Rare Classroom is designed for the curious reader who wants to get informed on

Doing What is Best For the Patient May Override a Doctor’s Compassion

Compassion [kuhm–pash-uhn] noun A feeling of deep sympathy and sorrow for another who is stricken by misfortune, accompanied by a strong desire to alleviate the

Study of the Week: Investigating The Origins of Adult T-Cell Leukemia/Lymphoma

Welcome to Study of the Week from Patient Worthy. In this segment, we select a study we posted about from the previous week that we

Rare Disease

Enzyme Images Help Solve Cause of Rare Neurodegenerative Diseases

According to a recent article, researchers were able to produce the first images of an enzyme that may figure out the unknown cause of a

Diffuse Large B-cell Lymphoma

First Patient Dosed in MVP-S, KEYTRUDA Study for DLBCL

According to a news release from immuno-oncology company IMV Inc., the first patient has been dosed in the Phase 2b VITALIZE clinical trial. During the

COVID-19

No Relationship Between COVID-19 Vaccine and Preterm Birth, Study Shares

Over the last two years, the COVID-19 pandemic has dominated the headlines. In 2021, vaccines became available to prevent severe COVID-19 infection. However, this has

Moebius Syndrome

Moebius Syndrome Awareness Day is January 24th!

Moebius Syndrome Awareness Day is January 24th! This event was created in 2011 by the Many Faces of Moebius Syndrome (MFOMS). It is now celebrated

Gastrointestinal Stromal Tumors

ICYMI: QINLOCK Approved in UK for GISTs

In late December 2021, biopharmaceutical company Deciphera Pharmaceuticals, Inc. (“Deciphera”) shared that its therapy QINLOCK (ripretinib) was approved in the United Kingdom. The treatment is

Neutropenia

The Long Road to FDA Approval of Plinabulin and G-CSF to Prevent Chemotherapy Induced Neutropenia

BeyondSpring Pharmaceuticals has issued a press release announcing that the FDA presented the company with a complete response letter pertaining to its drug plinabulin and

Spinocerebellar Ataxia

Family Raises SCA3 Awareness

The Klassen family is no stranger to the rare disease community. According to the Denver Post, Greg Klassen was first diagnosed with spinocerebellar ataxia type

Rare Disease

University of Maryland Doctors Transplant a Modified Pig’s Heart In a Human Patient

This week the Guardian reported that a pig’s heart, which was genetically modified, had been transplanted into a patient by doctors who were trying to save

Rare Disease

Castle Creek Biosciences Expands Their Cell and Gene Therapy Platform By Acquiring Novavita Thera Inc.

According to a recent article, Castle Creek Inc. has acquired Novavita Thera Inc. in an effort to expand its research and development efforts. Castle Creek

Glioblastoma

Could IL-7 Improve Glioblastoma Survival?

A glioblastoma diagnosis can be devastating. Currently, the 5-year survival rate is under 10%. This highly malignant cancer, which forms in the brain and spinal