As reported on PharmaBiz, Alebund Pharmaceuticals has announced the first patient has been enrolled and treated in a global Phase IIb clinical trial evaluating AP306,
As reported on Inside Precision Medicine, scientists have developed a way to spot a specific lung cancer mutation in just minutes instead of weeks, using
As reported on Business Wire, Delcath Systems has announced the enrollment and dosing of the first patient in its global Phase 2 DELUMA clinical trial,
Two of Intellia Therapeutics’ clinical trials that had been on hold since October 2025 have now been released by the FDA. The Agency initially issued
As reported on Pharmaceutical Business Review, Affinia Therapeutics has been granted orphan drug designation by the US Food and Drug Administration (FDA) for AFTX-201, an
As reported on Fierce BioTech, Johnson & Johnson has received U.S. Food and Drug Administration (FDA) clearance for its Ottava Robotic Surgical System, marking a
As reported on Science Daily, scientists have combined polymer-coated nanoparticles with therapeutic drugs for cancer treatment, including treatment for ovarian cancer. The nanoparticles target tumors
As reported by The Manila Times, Abeona Therapeutics has announced that Cincinnati Children’s Hospital Medical Center has been designated as the seventh Qualified Treatment Center
Medical device innovator Xeltis has officially kicked off the European commercial rollout of its novel vascular access implant, aXess™. The milestone was marked by the
The FDA has Completed Its Investigation of the Recent 2024 Deaths of Two Young Boys Due to Liver Failure. Acute failure of the liver has
The pharmaceutical company Grifols—has started dosing patients in the final stage (Phase 3) of two clinical trials. The company is trying to get approval to
Editor’s Note: This article was shared with us by our friends at the AAMDS International Foundation. To see the article in its original format, please
A newly reported case from Nanchang University suggests that efgartigimod, a neonatal Fc receptor (FcRn) blocker approved for generalized myasthenia gravis, may offer a promising
Merck has reported positive topline findings from the Phase 3 KEYNOTE-C93 trial, demonstrating that pembrolizumab (KEYTRUDA®) significantly extended progression-free survival (PFS) compared with standard platinum-based
If you or a loved one has ever survived a stroke, you know that the hardest part of the journey often begins after you leave
Editor’s Note: This article was originally written and submitted to us by Regina Portnoy. When people think about leadership in clinical research, they often think
Editor’s Note: This is part 2 of a 3-part caregiver story, submitted to us by Joan Foster, who was a caregiver for her husband Charles’
As reported on Inside Precision Medicine, for years, a chronic spinal cord injury (SCI) has felt like a permanent biological roadblock. When the spinal cord
"Sometimes the biggest difference between where you are and where you want to be is simply deciding to begin. The perfect time may never come, but every small step you take today brings you closer to the life you're working toward. Your future self will thank you for the courage you showed today.
✨Start before you're ready. Progress always begins with one step.✨
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From our friends IndousrareEarly bird registration is now open for the SIAMG–IndoUS Bridging RARE Summit 2026!
Join a global community of researchers, clinicians, healthcare professionals, patient advocates, industry leaders, and policymakers working together to advance rare disease research, innovation, diagnosis, and patient care.
👉 Secure your spot: www.siamg2026bangalore.com/indous-rare-summit.html
📅 December 10–13, 2026
📍 Shangri-La Bengaluru
Learn, collaborate, and help shape the future of rare disease care.
🌐 Learn more: www.indousrare.org/siamg/
#BridgingRARE #RareDiseaseSummit #IndoUSrare #SIAMG #Bridge4RARE #Roar4RARE #RareDiseaseAdvocacy #PatientAdvocacy #RareDiseaseCommunity
Thank you to Sierra Domb, for her incredible leadership of Visual Snow Initiative
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