Ebola
Ebola Continues To Be a Global Threat
A novel investigational Ebola vaccine has shown encouraging safety and immunogenicity results in a first-in-human clinical trial, supporting further development of an alternative vaccination strategy
Imfinzi–Imdelltra Combination Extends Survival in First-Line Extensive-Stage Small Cell Lung Cancer
- September 13, 2026
“Lead the Way” with Dustin Chapman
A New App for Duchenne Muscular Dystrophy Caregivers
FDA Authorizes Daraxonrasib for Metastatic Pancreatic Cancer After Positive Phase 3 Trial Results
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Rare Disease
TAVR Is Reaching Younger Patients. What Happens Decades Later?
Editor’s Note: Patient Worthy is honored to share this article, originally written by David St. Denis, President & Director at Anteris Technologies. Transcatheter aortic valve
Huntington's disease
The Researcher Who Would Not Be Tested
Although Nancy Wexler’s efforts were largely responsible for creating a genetic test to locate the Huntington’s gene, she refused to take the test herself saying
Breast Cancer
Guardant360 CDx Approved as Companion Diagnostic for AstraZeneca’s Etcamah in ESR1-Mutated Breast Cancer
As reported on Fierce BioTech, Guardant Health has secured U.S. Food and Drug Administration approval for its Guardant360 CDx liquid biopsy test as the companion
Rare Disease
Dual-Drug Strategy Shows Promise Against Treatment-Resistant Prostate Cancer
As reported on Science Daily, researchers at the University of Michigan have identified a potential new therapeutic approach for aggressive prostate cancers that become resistant
Multiple Myeloma
BMS Achieves Milestone with Next-Generation CAR-T Therapy for Multiply-Treated Myeloma Patients
GPRC5D-Targeting Approach Positions Company to Expand Post-BCMA Treatment Options As reported on Fierce BioTech, Bristol Myers Squibb announced positive results from its pivotal Quintessential trial
Rare Disease
To Stand Beside Suffering
Editor’s Note: We’re honored to share the following article from our friends at the Courageous Parents Network. To see this article in its original format,
Pompe Disease
Machine Learning Maps and Discovers Clinical Endpoints in Pompe Disease Using Real-World Data
Editor’s Note: Patient Worthy is honored to share this article from Rareatives, originally written by our friend Jessica Lynn. To see the article in its
Colorectal cancer
When the Silence Got Loud
Editor’s Note: Patient Worthy is honored to share this story from our friends at Elephants & Tea, originally written by Bill Phillips, a colorectal cancer
PTEN Hamartoma Tumor Syndrome
New PTEN Research Could Help Predict Cancer Risk in Rare Genetic Syndrome
A single genetic change can have dramatically different effects from one person to the next. That is the reality for people living with PTEN hamartoma
Diabetes Type 2
FDA Expands Mounjaro’s Label to Include Cardiovascular Risk Reduction in Type 2 Diabetes
As reported on QZ, the U.S. Food and Drug Administration has approved a new indication for Eli Lilly’s tirzepatide (Mounjaro), allowing the therapy to be
Polycythemia vera
FDA Clears Takeda’s Mimrylo for Polycythemia Vera, Introducing a Novel Treatment Option
As reported on MedCity News, the U.S. Food and Drug Administration has approved Takeda Pharmaceutical’s Mimrylo (rusfertide) for the treatment of erythrocytosis in adults with
Colorectal cancer
BioNTech Ends Phase 2 Trial of Personalized mRNA Therapy in High-Risk Colorectal Cancer
As reported on Drugs, BioNTech has decided to halt development of its Phase 2 BNT122-01 study investigating autogene cevumeran (BNT122/RO7198457) in patients with resected colorectal
Gastroesophageal junction carcinoma
Phase 3 HERIZON-GEA-01 Analysis Strengthens Survival Evidence for Zanidatamab-Based Regimens in HER2-Positive Gastroesophageal Cancer
As reported on PharmaBiz, BeOne Medicines has reported positive results from the second interim analysis of the phase 3 HERIZON-GEA-01 trial, further supporting the use
Leukemia
Think Beyond Remission to Protect the Life We Saved: A Young Man’s Journey with T-cell Acute Lymphoblastic Leukemia/Lymphoma
At 22, a young person’s world should be filled with possibilities—a career to build, places to travel, friendships to make, and a future to imagine.
Essential thrombocytosis
FDA Approves PharmaEssentia’s Besremi for Essential Thrombocythaemia
As reported on Pharmaceutical Technology, the US Food and Drug Administration (FDA) has granted approval to PharmaEssentia’s Besremi (ropeginterferon alfa-2b-njft) for the treatment of adults
Multiple Sclerosis
Novartis’ Remibrutinib Cuts Relapse Rates in Phase III Multiple Sclerosis Studies
In a recent press release, Novartis has reported positive topline results from its Phase III REMODEL-1 and REMODEL-2 trials, showing that the investigational oral Bruton’s
Metastatic Breast Cancer
EU Approves Enhertu Plus Pertuzumab for First-Line HER2-Positive Metastatic Breast Cancer
As reported on Business Wire, the European Commission has approved trastuzumab deruxtecan (Enhertu) in combination with pertuzumab for the first-line treatment of adults with unresectable
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Pessimism asks, "What if things don't get better?" Optimism asks, "What if they do?"
For patients facing serious illness, optimism isn't about ignoring reality. It's about holding space for hope while navigating uncertainty. Every treatment, every milestone, and every step forward starts with the belief that tomorrow can be better than today.
Hope may not change the diagnosis, but it can change how we face the journey. 💙
#Optimism #PatientAdvocacy #Hope #PatientWorthy
✨ Sometimes the journey you never expected becomes the one that gives your life the most purpose.
For years, Nick kept multiple sclerosis at arm’s length. But over time, he discovered that living with MS wasn't just part of his story, it became a source of strength, connection, and meaning.
In this inspiring Story Share, Nick opens up about his diagnosis, navigating symptoms like tingling and numbness, and finding purpose through building a community for others affected by MS. His message is a powerful reminder that whether you're newly diagnosed, years into your journey, or still figuring out what MS means for your life, you don't have to have all the answers today.
📖 Read Nick's full story on Patient Worthy:
patientworthy.com/2026/08/08/from-diagnosis-to-purpose-nicks-ms-journey/
🌐 Learn more about the ms life community: www.mslifecommunity.com
📸 Follow: @mslife. community
#MultipleSclerosis #MS #MSAwareness #LivingWithMS #PatientStory #PatientVoices #ChronicIllness #InvisibleIllness #MSSupport #MSCommunity #StrongerTogether #PatientWorthy #StoryShare
Some medical findings can provide especially important clues during the diagnostic process. A pathognomonic sign or symptom is strongly associated with a specific condition, helping healthcare providers distinguish it from other diseases with similar presentations. For people navigating complex or rare conditions, these distinctive findings can be an important piece of the diagnostic puzzle!
#rarewordoftheweek #raredisease #rarediseaseawareness #PatientWorthy
