Family That Lost Son To Krabbe Disease Pushes For Newborn Screening
Losing a child has to be one of the most heart-wrenching experiences a family can encounter, yet losing a child when it could have been
The LRRO’s mission is to maximise Health Care Resources, advance the world’s leading Research and to provide the premium support for all the Australasian Leukodystrophy families with the outcome being a cure. In fulfilling our mission our objectives are…
Losing a child has to be one of the most heart-wrenching experiences a family can encounter, yet losing a child when it could have been
You wouldn’t know by looking at 5-year-old Grayson Ledbetter that he only had a few years of life left to live. According to The Washington
Eva-Rose Sturgess is eighteen months old. She faces a disease for which there is no known cure: leukodystrophy. Her parents felt like their world came
A new treatment under development has produced promising results in patients with blood cancers and is now being tested in inherited metabolic disorders, reports Financial
According to a story from abc.net.au, ever since Massimo Damiani was first diagnosed with a leukodystrophy, his parents, Sally and Stephen, have been committed to
Meet Ruby, a beautiful 3 year old who was diagnosed with hypomyelination with atrophy of basal ganglia and cerebellum, or H-ABC, shortly after her birth. H-ABC
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