On July 8, 2021, gene therapy company Lysogene shared that its gene therapy candidate LYS-GM101, for patients with GM1 gangliosidosis, received Fast Track designation from the FDA. Currently, no treatments…
When I think of anxiety, I think of the movie, Gremlins (1984). For those of you who have seen this movie, you know that feeding a gremlin after midnight turns…
As reported in the Chicago Tribune; Jason Matthews spent his 69 years immersed in only the most thrilling of adventures. After three decades in the CIA, Matthews used eloquence and…
Aromatic L-Amino Acid Decarboxylase (AADC) DeficiencyWhat is aromatic l-amino acid decarboxylase deficiency?Aromatic l-amino acid decarboxylase (AADC) deficiency is a rare genetic disorder that occurs when the enzyme l-amino acid decarboxylase…
CureGRIN is investigating a new symptom of GRIN disorders, a group of rare genetic conditions that cause a wide variety of physical and intellectual symptoms. Referred to as neurostorms, this…
Jason Matthews, the author of the award-winning series Red Sparrow and former CIA officer, passed away on April 28th due to corticobasal degeneration. This rare, neurological condition causes the degeneration and…
Medical research is crucial to expanding an understanding of certain conditions, which ultimately leads to improved diagnostic and treatment options, and more social awareness. In a recent press release, CurePSP…
I think it would be safe to say that everyone is afraid of something. Sometimes the fear is justified and sometimes not. In this article, I want to focus on…
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