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FDA Green Lights Drugs for Two Rare Diseases  

FDA Green Lights Drugs for Two Rare Diseases  

  • Post author:Jean Martell
  • Post published:December 26, 2018
  • Post category:Blastic plasmacytoid dendritic cell neoplasm/paroxysmal nocturnal hemoglobinuria

Big news out of the FDA last week! Alexion Pharmaceuticals got approval for ALXN1210 for paroxysmal nocturnal hemoglobinuria, or PNH, which will now be sold as Ultomiris, while Stemline got approval…

Continue Reading FDA Green Lights Drugs for Two Rare Diseases  

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