Rare Disease
Why the Patient Perspective Must Play a Critical Role at the FDA
According to a story from the US Food and Drug Administration (FDA), Dr. Amy Abernethy, who is the current Prinicipal Deputy Commissioner at the agency,
Rare Patient News. Well Done.
Presentation Highlights Need for Improvements in Familial Hypercholesterolemia Care
- November 21, 2019
FDA Gives Rare Pediatric Disease Designation to Experimental Drug for Treating Rett Syndrome
Study Reveals New Approach for Diagnosing Nonalcoholic Steatohepatitis
A New Treatment for Cushing’s Syndrome Nears EU Approval
LATEST PATIENT WORTHY ARTICLES
Neuromyelitis Optica
Neuromyelitis Optica: A Year-Long Struggle to Regain Sight
According to a story from marieclaire.co.uk, Vanessa Potter, a TV producer, suddenly woke up one morning to realize that her eyesight was rapidly failing. That
ROHHAD
Boy With ROHHAD Earns Pride of Britain Award for Fundraising
According to a story from STV News, Aaron Hunter, who is nine years old and was born with the rare condition ROHHAD, recently earned the
Cystic Fibrosis
A Woman With Cystic Fibrosis and Another With Heart Failure Got Organ Transplants From the Same Donor
According to a story from theage.com.au, a remarkable turn of fate would bring together two women who would have otherwise never known each other—and save
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Lichen planus follicularis
Dermatologists Urge Caution When Using Skin Creams
An article by Dr. Syavra Tipirneni, dermatologist, recently appeared in BioSpectrum News. Dr. Tipirneni points out that we often succumb to our desire for
Idiopathic Pulmonary Fibrosis
NIH Commits Major Grant Funds Towards Idiopathic Pulmonary Fibrosis Study
According to a story from PR Newswire, the National Institutes of Health (NIH) and Three Lakes Partners have awarded a grant to the tune of
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PINNED POST
Why Are Adults in the US Having Trouble Accessing Their Medications?
Modern medication has the ability to save lives and improve living standards. However, medicine is less beneficial when patients’ prescribed treatments are delayed, and entirely
PW Collaborator
November 19, 2019
