Free Summit on Severe Combined Immunodeficiency (SCID) Coming Soon!
source: pixabay.com

Free Summit on Severe Combined Immunodeficiency (SCID) Coming Soon!

Severe Combined Immunodeficiency Severe combined immunodeficiency (SCID) is a group of diseases caused by mutations that affect how the immune system works to fight infections. These anomalies are usually passed…

Continue Reading Free Summit on Severe Combined Immunodeficiency (SCID) Coming Soon!
A Molecular Signature on Stressed Liver Cells Provides PSC Patients With A New Clue to Their Condition
source: pixabay.com

A Molecular Signature on Stressed Liver Cells Provides PSC Patients With A New Clue to Their Condition

The rare liver disease primary sclerosing cholangitis (PSC) may impact just .01% of people, but the extremely pernicious disorder's attacks on the liver mean bearers of the disorder account for…

Continue Reading A Molecular Signature on Stressed Liver Cells Provides PSC Patients With A New Clue to Their Condition
The FDA Approves An Expanded Chemotherapy Treatment For Acute Myeloid Leukemia to Include Children
source: pixabay.com

The FDA Approves An Expanded Chemotherapy Treatment For Acute Myeloid Leukemia to Include Children

  Cancer Network recently reported that Jazz Pharmaceuticals’ Vyxeos was approved by the FDA to treat therapy-related pediatric patients one year or older who were newly diagnosed with acute myeloid…

Continue Reading The FDA Approves An Expanded Chemotherapy Treatment For Acute Myeloid Leukemia to Include Children
Businesses Can Support Employees’ Participation in Clinical Trials and Change the Future of Research
source: pixabay.com

Businesses Can Support Employees’ Participation in Clinical Trials and Change the Future of Research

Financial Burdens in Rare Disease In 2019, 20% of all adults in the United States have reported that they had large medical bills that were unexpected. 18% currently had medical…

Continue Reading Businesses Can Support Employees’ Participation in Clinical Trials and Change the Future of Research
Doctor Urges His Colleagues to Apply Lessons from COVID-19 to Rare Diseases
source: pixabay.com

Doctor Urges His Colleagues to Apply Lessons from COVID-19 to Rare Diseases

  In a recent contribution to MSN, Dr. Christopher Austin, director of the NIH Advancing Translational Sciences, compared the medical community’s record-breaking approach to the COVID-19 pandemic with current efforts…

Continue Reading Doctor Urges His Colleagues to Apply Lessons from COVID-19 to Rare Diseases

Researchers Have Uncovered a Missing Link That May Lead to Development of Brain Disorder Treatments

For years, scientists have known the mechanisms underlying normal, as well as the disease-causing (pathogenic) versions, of prions. But according to a recent article published in Sci-Tech Daily, no one…

Continue Reading Researchers Have Uncovered a Missing Link That May Lead to Development of Brain Disorder Treatments
Make Research Remote, Hear Rare Voices`
source: pixabay.com

Make Research Remote, Hear Rare Voices`

As the pandemic shifted cocktail hour onto zoom and professors posted their full course material online, many rare patients reveled. Not because we weren’t suffering through the pandemic too, but…

Continue Reading Make Research Remote, Hear Rare Voices`
Despite the Pandemic, 2020 Had More Drug Development for Rare Diseases than 2019
Sourced from publicdomainpictures.net (https://www.publicdomainpictures.net/en/view-image.php?image=275669&picture=chemical-research)

Despite the Pandemic, 2020 Had More Drug Development for Rare Diseases than 2019

Rare Disease Day is February 28th. This year, it caused a lot of reflection among healthcare professionals and families impacted by rare conditions. How has the pandemic shifted progress in…

Continue Reading Despite the Pandemic, 2020 Had More Drug Development for Rare Diseases than 2019

Oncology Researchers Are Beginning to Focus on Ways to Stop Uncontrolled Cancerous Cell Division

According to a recent article in Fierce Biotech, most cancers progress through constant cell division. Scientists at Vanderbilt University are determined to find the reason for this mysterious cell division.…

Continue Reading Oncology Researchers Are Beginning to Focus on Ways to Stop Uncontrolled Cancerous Cell Division