Incyte Reports Positive Phase III Results for Tafasitamab in First-Line DLBCL Treatment
- January 7, 2026
Repurposing Breast Cancer Drug Offers New Hope for Acute Myeloid Leukemia Patients
Living with gMG: Lessons from William, a Nurse and Patient
FDA Approve Drug That Targets Root Cause of Life-Threatening Kidney Disease Affecting Children and Young Adults
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#mytonicdystrophy #clinicaltrialResearchers at Sanofi are recruiting adults with non-congenital myotonic dystrophy type 1 for a phase 1/2 clinical trial evaluating an investigational gene therapy. 🧬💪
The study will assess the safety of SAR446268 and its potential to target the toxic RNA that drives DM1. Participants will receive a single IV infusion and be followed over two years.
Learn who may be eligible and what participation involves. 👉 mdaquest.org/clinical-research-alert-phase-1-study-of-gene-therapy-in-individuals-with-myotonic-d...
#MyotonicDystrophy #DM1 #ClinicalTrials #GeneTherapy #RareDisease #Research
@csnk2a1foundation.org What a line-up of support ! Mark your calendars today.!🗓️ SAVE THE DATES! 🗓️
Join us throughout 2026 for our bi-monthly OCNDS Family Zoom Meetings hosted by our Parent Advisory Board. Together, we’ll discuss successes, challenges, and all things OCNDS.
👉 Please note: These meetings are only for primary caregivers, guardians, and those living with OCNDS.
👉 We will be using AI technology for live-caption translation—most languages are supported.
👉 Meetings are always held at 08:00 AM Pacific Time (US & Canada) over Zoom.
2026 Family Zoom Meeting Dates
Sunday, February 8 – loom.ly/YOMNi9Q
Saturday, April 18 – loom.ly/-vFIho4
Sunday, June 14 – loom.ly/vONpS7k
Saturday, August 15 – loom.ly/gi5gNj4
Sunday, October 25 – loom.ly/V5ACR8g
Saturday, December 12 – loom.ly/_0jobm8
After registering, you will receive a confirmation email with details for joining the meeting.
💙💚 We look forward to connecting with you throughout 2026!
#ocnds #csnk2a1 #hopeintoaction #timeisnow #BoldBreakthroughs
@CureDucheneOne of the most anticipated experiences of FUTURES 2026 is back: the Discovery Cove dolphin swim.💙
Secure your spot for our exclusive Discovery Cove Family Excursion! Space is limited, and early registration gives you the best chance to enjoy this unforgettable Orlando experience. (Dolphin interactions are limited and not guaranteed — but registering now gets you in line!)🤩
Register now: web.cvent.com/event/ee9e7402-2c59-420f-9cf9-5731cf20d4d9/summary
#dmd#duchenne#dolphin#orlando
