Oral FGFR Inhibitor Shows Promise for Children With Achondroplasia
Research Opportunities in Ataxia and Movement Disorders
Choosing Joy: Erika’s Journey of Raising a Child with Dravet Syndrome, a Rare Form of Epilepsy
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ADHD management isn't one-size-fits-all, it's a mix of medication, therapy, lifestyle adjustments, and support tailored to you. Finding what works takes time, but research shows combining approaches works best. You've got this! #adhd #ADHDTreatment #mentalhealthawareness #ADHDManagement #PatientWorthy
#shareyourstory with us here: bit.ly/4dV7gru
A new stem-cell-based gene therapy offers hope for patients living with Hunter syndrome, as this one-time treatment could potentially extend the lives of those living with the condition. Read more here:
patientworthy.com/2026/01/25/one-time-gene-therapy-offers-new-hope-for-hunter-syndrome/
Today is Alagille Awareness Day, a time to shed light on this rare genetic condition while supporting the individuals and families living with this complex condition.
The multi-colored awareness ribbon reflects the many ways Alagille Syndrome can affect the body:
💛 Yellow- liver & digestive systems
❤️ Red- heart & circulatory
💚 Green- kidneys
💙 Blue- lungs
💜 Purple- brain and vascular
🩶 Cream- skeletal
All together, the colors symbolize unity, diversity of symptoms, and hope in the ALGS community!
Share your ALGS story with us here: bit.ly/4dV7gru
And visit Alagille Syndrome Alliance for more info!
#ALGSAwarenessDay #AlagilleSyndrome #PatientWorthy
