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4 days ago

Patient Worthy
#RettSyndromeRNA editing is a promising technique for correcting certain point mutations but needs careful control to achieve accuracy. In this recently published study based on research funded in part by IRSF, researchers applied a novel strategy to enhance RNA editing’s precision and prevent undesirable, random editing. This approach proved successful in restoring normal MeCP2 in the brain of Rett mice, paving the way for RNA editing as a potential genetic therapy for Rett syndrome in the future. Read the article: www.nature.com/articles/s41587-024-02313-0 ... See MoreSee Less
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