Rare Classroom: Williams Syndrome
Welcome to the Rare Classroom, a new series from Patient Worthy. Rare Classroom is designed for the curious reader who wants to get informed on
- Rare Disease News
- contribute@patientworthy.com
Remembering Rachael Kaflowitz: One Mother’s Fight to Support NPC Research and Awareness (Pt. 3)
- December 1, 2021
RGX-202 for DMD Earns Orphan Drug Designation
A Five Year $2.25M Grant Has Been Awarded for the Study of Alport Syndrome
Study: Telotristat Ethyl Improves Symptoms in Carcinoid Syndrome Patients
PODCAST: WAIT, HOW DO YOU SPELL THAT?
PATIENT WORTHY SERIES
Rare Classroom: Acalvaria
Welcome to the Rare Classroom, a new series from Patient Worthy. Rare Classroom is designed for the curious reader who wants to get informed on
Science Simplified: What is Gene Therapy?
Want to learn about scientific topics without needing a PhD? Check out the Science Simplified blog from TESS Research Foundation! Dr. Tanya Brown, PhD, works
Study of the Week: The High Cost Burden of Rare Diseases
Welcome to Study of the Week from Patient Worthy. In this segment, we select a study we posted about from the previous week that we
THE LATEST FROM PATIENT WORTHY
Head and neck cancer
Mouth Cancer Awareness Month Demands More Attention Than You May Think
Written by Dr. Lauren Steddum So far in 2021, more than 54,000 people have been diagnosed with oral cavity and oropharyngeal cancer and nearly 11,000
Neuromyelitis Optica
CHMP Recommends Approval for UPLINZA to Treat NMOSD
Back in June of this year, the FDA granted approval to UPLINZA to reduce attacks in patients with anti-aquaporin-4 immunoglobulin G seropositive (AQP4-IgG+) neuromyelitis optica
Eosinophilic Esophagitis
First Patient Dosed in ESO-101 Trial for EoE
It is always exciting to see the onset of a new clinical trial designed to research therapies to fill unmet needs for patients. According to
Necrotizing fasciitis
Former Hawks President Infected with Necrotizing Fasciitis in Florida
In the sports world, former Atlanta Hawks president Bob Williams has been known for his tenacity – but according to Newsweek, he may soon be
Acalvaria
Rare Classroom: Acalvaria
Welcome to the Rare Classroom, a new series from Patient Worthy. Rare Classroom is designed for the curious reader who wants to get informed on
Multiple Myeloma
Older Multiple Myeloma Patients Shouldn’t be Denied Transplants Solely Based on Age
Many doctors have thought in the past that age should be an automatic ineligibility factor for multiple myeloma patient transplants. However, Dr. Langren, Dr. Gasparetto,
Diffuse Large B-cell Lymphoma
DPX Delivery Platform Could Improve Care For Many Rare Cancers
IMV Inc. recently presented two posters at the AACR-NCI-EORTC Virtual International Conference on Molecular Targets and Cancer Therapeutics showcasing their DPX delivery platform’s immunotherapeutic capabilities.
Myasthenia Gravis
An Unprecedented Patient-Led Report on Myasthenia Gravis
On October 27, 2021, PR Newswire highlighted an article about a unique patient-led analysis that was conducted in Atlanta, Georgia, and Brussels, Belgium by people
Malignant pleural mesothelioma
Durvalumab Hopes to be Treatment Option for Malignant Pleural Mesothelioma
According to a recent article from OncologyLive, investigators are looking at durvalumab to aid in the treatment of adults with malignant pleural mesothelioma in the
Rare Disease
Metastatic NSCLC Survival Boosted by Dual Immunotherapy
According to a recent article, the overall survival of patients with untreated metastatic non-small cell lung cancer (NSCLC) were significantly improved by the addition
OF INTEREST
GET INVOLVED
