Treating Rett Syndrome: Clare’s Rare Patient Story
The joy of watching your child grow and meet developmental milestones is not always granted to some parents. Clare’s mother, Allison, described her emotions to
Here is a list of conditions this partner raises awareness and advocacy for:
The joy of watching your child grow and meet developmental milestones is not always granted to some parents. Clare’s mother, Allison, described her emotions to
Stoke Therapeutics and Acadia Pharmaceuticals made a joint announcement this week through Business Wire of their collaboration in the development of RNA-based medicines to potentially
It’s no secret that smoking tobacco can have some adverse effects on our health. But what kind of effects does smoking have while someone is
Holden and Elliot have felt a surge of support from their community recently, as their preschool came together to celebrate them and show their love.
Rare disease research faces many obstacles: lack of participants, lack of funding, and lack of interest are just a few. Now, the charity Cerebra has
Front Line Genomics has recently interviewed Dr. Michelle Krishnan, who is the Translational Medicine Leader in Rare Diseases at Roche. She focuses on rare neurodevelopmental
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