CysticLife
Condition Awareness & Advocacy
Here is a list of conditions this partner raises awareness and advocacy for:
Patient Worthy Posts on Cystic Fibrosis
Come On Pharma: It’s Not That Much of a Sacrifice to Study One Rare Disease Pro-Bono
At the heart of rare disease treatments is research. Currently, 95% of all rare diseases still have no approved therapies. Although there has been an
Potential Treatment for Cystic Fibrosis Displays Encouraging Interim Data
According to a story from Drug Development Technology, the drug developer Translate Bio has recently reported interim results from its phase 1/2 clinical trial. This
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DNA Sequencing Took Years, Now it Takes Hours; As a Result, Researchers Have Discovered The Cause of Four Rare Diseases
Researchers at the University of Tokyo have discovered that one segment of DNA is responsible for four rare diseases. As reported in Science Daily, the
In The UK, Improving Treatment Access for Rare Disease Patients is Critical
According to a story from Raconteur, as many as 3.5 million people living in the UK are expected to affected by some type of rare
European Medicines Agency Grants Experimental Cystic Fibrosis Drug Orphan Drug Designation
According to a press release from Aridis Pharmaceuticals, the Company has received Orphan Drug designation from the European Medicines Agency for its experimental cystic fibrosis-related
‘New Drug Application’ Filed to FDA for Cystic Fibrosis Treatment
Vertex Pharmaceuticals announced the submission of a New Drug Application (NDA) to the FDA for the VX-445 (elexacaftor), tezacaftor and ivacaftor triple combination regimen for
