Why Gene Therapy Can be a Boom or Bust for ADA Patients
Have you ever heard of “ex vivo” gene therapy? If you haven't, it means removing some cells, modifying them, and putting them back in. The goal? Curing the diseases that…
Have you ever heard of “ex vivo” gene therapy? If you haven't, it means removing some cells, modifying them, and putting them back in. The goal? Curing the diseases that…
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Doctor, por favor revise la sangre de mi bebé! La IDF alienta a los funcionarios estatales del estado de Louisiana a firmar en rutinas de detección de recién nacidos…
Cuando me uní a otros millones de fans obsesionados que veían lo que ha sido la popular episodio "Bubble Boy" en Seinfeld en 1992, no tenía ni idea de que…
Adenosine Deaminase (ADA) DeficiencyWhat is Adenosine deaminase (ADA) deficiency?Adenosine deaminase (ADA) deficiency is an inherited genetic disorder that causes damage to the immune system. ADA deficiency leads to something known…
It takes an average of seven years for a patient with a rare disease like severe combined immunodeficiency (SCID) to receive a correct diagnosis; and that comes after the patient…
What if you had an inherited disorder that caused a fat called globotriaosylceramide to build up in your cells? Chances are pretty good that you'd be diagnosed with Fabry disease,…
2015 Conferencia Nacional de la FDI se acerca rápidamente! Durante 3 días, Louisiana dará la bienvenida a las FDI y todos sus componentes y colaboradores. A partir del jueves, de…