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Is the FDA Approving Drugs too Quickly?

Is the FDA Approving Drugs too Quickly?

   At times there seems to be no happy medium in life. A recent article in Bloomberg claims that the speed at which the FDA is approving newly developed drugs is…

Continue Reading Is the FDA Approving Drugs too Quickly?
Gene Therapy Being Assessed for Treatment of X-Linked Severe Combined Immunodeficiency

Gene Therapy Being Assessed for Treatment of X-Linked Severe Combined Immunodeficiency

  Mustang Bio, a biopharmaceutical company, has been working with St. Jude Children's Research Hospital to develop MB-107, a lentiviral gene therapy to treat X-linked severe combined immunodeficiency. Mustang Bio…

Continue Reading Gene Therapy Being Assessed for Treatment of X-Linked Severe Combined Immunodeficiency
Early Data Looks Encouraging for an Experimental Thalassemia Treatment

Early Data Looks Encouraging for an Experimental Thalassemia Treatment

According to a story from globenewswire.com, the drug developer Agios Pharmaceuticals, Inc. has recently released a preliminary analysis of phase 2 trial findings that have served to establish proof-of-concept for…

Continue Reading Early Data Looks Encouraging for an Experimental Thalassemia Treatment
How Gene Therapy is Being Applied to Sickle Cell Disease

How Gene Therapy is Being Applied to Sickle Cell Disease

  Grajevis Bakatunkanda lived in the Democratic Republic of the Congo, where he received treatment for malaria after experiencing weekly pain crisis. The treatment he received did not work, as…

Continue Reading How Gene Therapy is Being Applied to Sickle Cell Disease
How Researchers Used Multiple Sclerosis to Understand Autoimmune Encephalitis

How Researchers Used Multiple Sclerosis to Understand Autoimmune Encephalitis

  Autoimmune encephalitis is a group of diseases that was only identified about a decade ago. The newness of this condition makes it difficult to completely understand it. Dr Robb…

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Pierre Robin Sequence: EU Family Seeks Appeal After Denial of Treatment Coverage

Pierre Robin Sequence: EU Family Seeks Appeal After Denial of Treatment Coverage

Philippe Pakter’s daughter Lysiane was born on March 29th 2017 in Lyon, France. However, soon after her birth, Philippe and his partner Delphine were hit with shocking news: Lysiane was…

Continue Reading Pierre Robin Sequence: EU Family Seeks Appeal After Denial of Treatment Coverage
The Results From This Immune Thrombocytopenia Trial are Good News for Patients

The Results From This Immune Thrombocytopenia Trial are Good News for Patients

According to a story from ucb.com, the biopharmaceutical company UCB has recently released the final results from its phase 2 clinical trial which tested the company's investigational monoclonal antibody rozanolixizumab…

Continue Reading The Results From This Immune Thrombocytopenia Trial are Good News for Patients
A Recent Trial Found the Drug Rinvoq Can be Effective Treatment for Ankylosing Spondylitis

A Recent Trial Found the Drug Rinvoq Can be Effective Treatment for Ankylosing Spondylitis

According to a story from Ankylosing Spondylitis News, the results of a recent phase 2/3 clinical trial indicate that the drug upadacitinib (marketed as Rinvoq) can be an effective treatment…

Continue Reading A Recent Trial Found the Drug Rinvoq Can be Effective Treatment for Ankylosing Spondylitis
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You Are Not Alone: Empowering the Advanced Kidney Cancer Community
Finding Light Through Story-The Power of Ambassadorship in the Endometrial Cancer Community
*cancer that cannot be removed with surgery or has spread to other parts of the body. GEJ= gastroesophageal junction (where the esophagus joins the stomach)
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