PTC Therapeutics has just announced data from the very first study which examined how taking care of a child diagnosed with aromatic L-amino acid decarboxylase (AADC) deficiency can impact caregivers.…
COVID-19 long-haulers, now called Post-Acute Sequelae of SARS-CoV-2 Infection, or PASC, have often been compared to myalgic encephalomyelitis/chronic fatigue syndrome (ME/CFS). However, there wasn't a study directly comparing these two…
According to a story from Parkinson's News Today, a small study recently demonstrated that fecal transplants could help relieve gastrointestinal problems in Parkinson's disease patients, as well as reducing the…
A recent study has found that Lambert-Eaton Myasthenic Syndrome (LEMS), a rare disease, could also be linked to another rare condition- Merkel cell carcinoma (MCC) which is a type of…
According to MedPage Today, data from a preliminary study evaluating SHR0302, an investigational Janus kinase 1 (JAK1) inhibitor, showed promise for treating patients with moderate-to-severe atopic dermatitis (AD). Following treatment,…
In a study published on Hindawi, a group of patients with severe cystic fibrosis that were awaiting a lung transplant underwent a telerehabilitation program to maintain their lung function. The…
On March 6, 2021, biopharmaceutical company Altavant Sciences ("Altavant") shared that it had initiated its Phase 2b ELEVATE 2 clinical trial. During the trial, researchers will evaluate rodatristat ethyl ("rodatristat")…
Brickell Biotech has just announced the findings from their Phase 3 study investigating the long-term efficacy and safety of sofpironium bromide gel for the treatment of primary axillary hyperhidrosis. Hyperhidrosis…
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