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Another Amyotrophic Lateral Sclerosis Trial Fails to Achieve Endpoints

Another Amyotrophic Lateral Sclerosis Trial Fails to Achieve Endpoints

According to a story from BioPharma Dive, Apellis Pharmaceuticals will now join the ranks of pharma companies that have seen an investigational therapy being developed for amyotrophic lateral sclerosis falter…

Continue Reading Another Amyotrophic Lateral Sclerosis Trial Fails to Achieve Endpoints
FDA Panel Backs Approval of a New Drug for Alzheimer’s

FDA Panel Backs Approval of a New Drug for Alzheimer’s

  The FDA advisory panel which is composed of specialists who advise the FDA on brain medications, recently voted 6-0 in agreement on that the new drug, Leqembi, was effective…

Continue Reading FDA Panel Backs Approval of a New Drug for Alzheimer’s
Bispecific T-Cell Redirection Antibodies in the Treatment of Multiple Myeloma

Bispecific T-Cell Redirection Antibodies in the Treatment of Multiple Myeloma

Patients who have been heavily pretreated for relapsed/refractory multiple myeloma participated in the phase 2 study of bispecific T cell redirection antibodies. The participants responded to treatment with a combination…

Continue Reading Bispecific T-Cell Redirection Antibodies in the Treatment of Multiple Myeloma
Bylvay Now Approved for Cholestatic Pruritus Caused by Alagille Syndrome in Patients Aged 1+ 

Bylvay Now Approved for Cholestatic Pruritus Caused by Alagille Syndrome in Patients Aged 1+ 

Have you ever had an itch that you just can't seem to scratch? Intensely itchy skin, also known as pruritus, is a hallmark characteristic of many conditions that affect the…

Continue Reading Bylvay Now Approved for Cholestatic Pruritus Caused by Alagille Syndrome in Patients Aged 1+ 
Peptide Shows Potential for Treating Eosinophilic Esophagitis in Phase 2 Trial

Peptide Shows Potential for Treating Eosinophilic Esophagitis in Phase 2 Trial

According to a story from Healio, the pharmaceutical company Revolo Biotherapeutics has been developing '1104, a peptide with a mechanism that 'resets' the immune system to pre-empt the appearance of…

Continue Reading Peptide Shows Potential for Treating Eosinophilic Esophagitis in Phase 2 Trial
Interim Results Available on LL-BMT1 for Glaucoma

Interim Results Available on LL-BMT1 for Glaucoma

About 150,000 people with glaucoma across the United States wear contact lenses—and they may soon have access to an even more effective wearable treatment option.  According to Medical Device Network,…

Continue Reading Interim Results Available on LL-BMT1 for Glaucoma
Interim Data Available on mRNA-3927 for Propionic Acidemia

Interim Data Available on mRNA-3927 for Propionic Acidemia

  Children born with propionic acidemia require life-long treatment and care; without it, this disorder can lead to coma or even death. While there are supportive treatment options, no current…

Continue Reading Interim Data Available on mRNA-3927 for Propionic Acidemia
Updated Interim Analysis of AIR Trial Shows C21 Promise for IPF

Updated Interim Analysis of AIR Trial Shows C21 Promise for IPF

  Currently, there are two FDA-approved treatments for people living with idiopathic pulmonary fibrosis (IPF): Ofev (nintedanib) and Esbriet (pirfenidone). While these therapies are effective in improving lung function, they…

Continue Reading Updated Interim Analysis of AIR Trial Shows C21 Promise for IPF
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The Mentor She Wished She Had - How Elizabeth Became a Lifeline for EB
Finding Strength Together: Scott and Katie’s Journey with Advanced Kidney
You Are Not Alone: Empowering the Advanced Kidney Cancer Community
Finding Light Through Story-The Power of Ambassadorship in the Endometrial Cancer Community
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