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BMN 307

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BMN 307 Trial for PKU Stopped Over Safety Issues
TheDigitalArtist / Pixabay

BMN 307 Trial for PKU Stopped Over Safety Issues

  • Post author:Jessica Lynn
  • Post published:September 28, 2021
  • Post category:Phenylketonuria/pku

Unfortunately, clinical trials do not always proceed the way that drug developers - and patients - hope. For example, an ongoing Phase 1/2 clinical trial evaluating BMN 307, an investigational…

Continue Reading BMN 307 Trial for PKU Stopped Over Safety Issues
Investigational PKU Treatment BMN 307 Given Fast Track Designation
PublicDomainPictures / Pixabay

Investigational PKU Treatment BMN 307 Given Fast Track Designation

  • Post author:Jessica Lynn
  • Post published:October 6, 2020
  • Post category:Phenylketonuria/pku

On October 2, 2020, biotechnology company BioMarin Pharmaceutical ("BioMarin") announced that its investigational gene therapy candidate BMN 307 received the Fast Track designation from the FDA. The therapy is designed…

Continue Reading Investigational PKU Treatment BMN 307 Given Fast Track Designation
Finding Light Through Story-The Power of Ambassadorship in the Endometrial Cancer Community
*cancer that cannot be removed with surgery or has spread to other parts of the body. GEJ= gastroesophageal junction (where the esophagus joins the stomach)
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