Jessica Lynn has an educational background in writing and marketing. She firmly believes in the power of writing in amplifying voices, and looks forward to doing so for the rare disease community.

    Clinical Trial to Evaluate HMI-103 for PKU
    source: pixabay.com

    Clinical Trial to Evaluate HMI-103 for PKU

    Previously, clinical-stage genetic medicines company Homology Medicines, Inc. ("Homology") submitted an Investigational New Drug (IND) application to the FDA for HMI-103, an investigational gene editing therapy designed to treat phenylketonuria…

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    Crizanlizumab for SCD is Coming to England
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    Crizanlizumab for SCD is Coming to England

    According to The Guardian, England’s National Health Service (NHS) has announced that a new therapeutic option will be available for patients with sickle cell disease (SCD). This treatment, called crizanlizumab,…

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    ATYR1923 Safe and Effective for Pulmonary Sarcoidosis
    Photo by Robina Weermeijer on Unsplash

    ATYR1923 Safe and Effective for Pulmonary Sarcoidosis

    Clinical trials can be helpful tools in determining the safety, efficacy, tolerability, recommended dose, and pharmacokinetics of specific drugs (among other things). In doing so, these trials help tell researchers…

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    India Develops Silicosis Screening Test
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    India Develops Silicosis Screening Test

    Silica is a naturally occurring substance found in various types of rocks, clay, and sand. Unfortunately, when this silica dust is inhaled, especially over long periods of time, it can…

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    October is Spina Bifida Awareness Month!
    Source: https://www.spinabifidaassociation.org/blog/10awarenessmonth2021/

    October is Spina Bifida Awareness Month!

    Did you know—October is known as Spina Bifida Awareness Month, with October 25 being designated as World Spina Bifida and Hydrocephalus Day? That means, all October long, you can help…

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    New Collaboration to Develop REV-0100 for Stargardt Disease
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    New Collaboration to Develop REV-0100 for Stargardt Disease

    Sometimes, companies work together to develop the best therapeutic options for patients. According to Optical Prism, biopharmaceutical company reVision Therapeutics, Inc. and specialty pharmaceutical company Aequus Pharmaceuticals Inc. recently joined…

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    Grandma Raises Spinal Muscular Atrophy Awareness After Grandson’s Death
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    Grandma Raises Spinal Muscular Atrophy Awareness After Grandson’s Death

    When Rhonda Stevey met her grandson, Koehyn, she was immediately smitten. The grandmother, who lives in Ohio, felt like her grandson was the happiest infant she had ever met. Unfortunately,…

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    Pirtobrutinib Shows Promise for Previously Treated CLL, SLL
    Photo by Paweł Czerwiński on Unsplash

    Pirtobrutinib Shows Promise for Previously Treated CLL, SLL

    The 2021 Society for Hematological Oncology (SOHO) Annual Meeting took place last month from September 8-11, 2021. During the meeting, researchers discussed new advances in the field of hematology. According…

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