Jessica Lynn has an educational background in writing and marketing. She firmly believes in the power of writing in amplifying voices, and looks forward to doing so for the rare disease community.

    Approvals Granted to Begin LYS-GM101 Clinical Trial for GM1 Gangliosidosis
    source: pixabay.com

    Approvals Granted to Begin LYS-GM101 Clinical Trial for GM1 Gangliosidosis

    In an exciting press release, gene therapy platform company Lysogene announced that it had received approval from the Medicines and Healthcare products Regulatory Agency (MHRA) and Research Ethics Committee. As…

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    DNMT3B Gene May Cause Pulmonary Hypertension, PAH Development
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    DNMT3B Gene May Cause Pulmonary Hypertension, PAH Development

    Recently, Pulmonary Hypertension News shared some burgeoning medical news: that the DNMT3B gene has now been linked to the development of pulmonary hypertension (PH) and a rare form of chronic high blood…

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    New Data Available for GSD1a, OTC Deficiency, and Wilson Disease Studies
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    New Data Available for GSD1a, OTC Deficiency, and Wilson Disease Studies

      In a recent press release, biopharmaceutical company Ultragenyx Pharmaceutical Inc. ("Ultragenyx") shared positive safety and efficacy data from Phase 1/2 clinical trials on gene therapy solutions for ornithine transcarbamylase…

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    Patients to Be Recruited Into ASLAN004 Expansion Cohort for Atopic Dermatitis
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    Patients to Be Recruited Into ASLAN004 Expansion Cohort for Atopic Dermatitis

      In a recent press release, biopharmaceutical company ASLAN Pharmaceuticals ("ASLAN") announced that it would begin recruiting patients for an expansion cohort of a clinical trial evaluating ASLAN004 for patients…

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    FDA Designations Granted to PRAX-222, PRAX-562 for Epileptic Encephalopathies
    Source: Pixabay.com

    FDA Designations Granted to PRAX-222, PRAX-562 for Epileptic Encephalopathies

    According to a recent press release from biopharmaceutical company Praxis Precision Medicines ("Praxis"), two of the company's drug candidates received either Orphan Drug or Rare Pediatric Disease designations for rare…

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    Elite Gamer Holiday Charity Tournament Raises $42K for Cure Rare Disease
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    Elite Gamer Holiday Charity Tournament Raises $42K for Cure Rare Disease

    Looking for a feel-good story? Then look no further. In December, telecom company Cox worked to make a difference for the rare disease community. The organization headed its Elite Gamer…

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