casimersen – Patient Worthy

FDA Accepts Casimersen NDA for Patients with Exon 45 Amenable DMD

Post author:Jessica Lynn
Post published:August 31, 2020
Post category:Duchenne Muscular Dystrophy

Earlier this week, Sarepta Therapeutics announced that the FDA approved a New Drug Application (NDA) for Casimersen (SRP-4045). The treatment, for patients with exon 45 amenable Duchenne muscular dystrophy (DMD),…

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