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First Gene Therapy Clinical Trial for Cystinosis Enrolling Soon

First Gene Therapy Clinical Trial for Cystinosis Enrolling Soon

  • Post author:Trudy Horsting
  • Post published:January 21, 2019
  • Post category:Cystinosis/Friedreich ataxia

Cystinosis Cystinosis is a rare disease which is caused by a buildup of cystine in the body's cells. This buildup impacts various organs including the brain, eyes, liver, kidneys, and muscles.…

Continue Reading First Gene Therapy Clinical Trial for Cystinosis Enrolling Soon
The Power of the Purple Crayon for Cystinosis Research
https://pixabay.com/en/child-girl-blond-face-view-amazed-659283/

The Power of the Purple Crayon for Cystinosis Research

  • Post author:Erica Zahn
  • Post published:May 31, 2017
  • Post category:Cystinosis/Rare Disease

Have you ever heard of the children’s book, Harold and the Purple Crayon? It’s about a little boy who draws the things he wants to see with his purple crayon,…

Continue Reading The Power of the Purple Crayon for Cystinosis Research

2017 CRF Day of Hope Family Conference

  • Post author:Patient Worthy Contributor
  • Post published:March 30, 2017
  • Post category:

The Cystinosis Research Foundation Day of Hope Family Conference registration closes on March 17th! So register now.

Continue Reading 2017 CRF Day of Hope Family Conference
CRF Grants Support the Quest for a Cure

CRF Grants Support the Quest for a Cure

  • Post author:Patient Worthy Contributor
  • Post published:February 24, 2017
  • Post category:Cystinosis/Timely

The Cystinosis Research Foundation is the largest provider of grants for cystinosis research. When we say largest we don't mean in the country, we mean in the world. In fact,…

Continue Reading CRF Grants Support the Quest for a Cure
Research for a Cystinosis CURE is Gaining Traction Thanks to the CRF
Pixabay

Research for a Cystinosis CURE is Gaining Traction Thanks to the CRF

  • Post author:Erica Zahn
  • Post published:November 10, 2016
  • Post category:Cystinosis/Rare Disease

It was a match made in heaven when the Homecoming King fell in love with the Homecoming Queen. Several years after they accepted their crowns, they got married and planned…

Continue Reading Research for a Cystinosis CURE is Gaining Traction Thanks to the CRF
Finding Light Through Story-The Power of Ambassadorship in the Endometrial Cancer Community
*cancer that cannot be removed with surgery or has spread to other parts of the body. GEJ= gastroesophageal junction (where the esophagus joins the stomach)
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