cysteamine – Patient Worthy

source: pixabay.com

Early Success in Trials for Experimental Gene Therapies for Fabry Disease and Cystinosis

Post author:Sunniva Bean
Post published:June 24, 2020
Post category:Cystinosis Fabry Disease Rare Disease

As reported in Business Fortnight, the top level gene therapy company AVROBIO has announced successful clinical trials for investigational drugs for Fabry disease and cystinosis. The CEO of AVROBIO, Geoff…

CLICK HERE TO SHARE YOUR STORY!

We believe rare disease patients are people, not a diagnosis. Through education, awareness and some humor, we help patients, caregivers and support persons by providing relevant and often inspirational news and stories.

Our goals are to share stories, cultivate strong community, provide the latest medical findings, connect people and pioneer production of patient worthy information. Help us attain these goals by telling us a little bit about yourself!

Let’s Work Together!

Keep Up to Date

Learn More