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GNEM

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Will Today’s Patients See a Treatment That Will End GNEM in Our Lifetime? Part Two

Will Today’s Patients See a Treatment That Will End GNEM in Our Lifetime? Part Two

  • Post author:Patient Worthy Contributor
  • Post published:May 26, 2022
  • Post category:GNE Myopathy

Continued From Part One He cannot participate in the sports and physically demanding hobbies he once enjoyed. “Due to pool & gym closures during the Covid pandemic, walking was my…

Continue Reading Will Today’s Patients See a Treatment That Will End GNEM in Our Lifetime? Part Two
Will Today’s Patients See a Treatment That Will End GNEM in Our Lifetime? Part One

Will Today’s Patients See a Treatment That Will End GNEM in Our Lifetime? Part One

  • Post author:NDF
  • Post published:May 25, 2022
  • Post category:GNE Myopathy

  I’ve known people to almost faint at the mention of words like “cancer,” “heart disease,” or “dementia,” imagining the uncertainty of one’s fate when confronted with these awful diseases.…

Continue Reading Will Today’s Patients See a Treatment That Will End GNEM in Our Lifetime? Part One
New Plans for Human Dosing in GNE Myopathy Trial
mcmurryjulie / Pixabay

New Plans for Human Dosing in GNE Myopathy Trial

  • Post author:Kendall Mason
  • Post published:September 20, 2021
  • Post category:GNE Myopathy

There are now plans in place to study a gene therapy for GNE myopathy (GNEM), with human dosing expected to begin in 24 months. The plans were developed by the…

Continue Reading New Plans for Human Dosing in GNE Myopathy Trial
You Are Not Alone: Empowering the Advanced Kidney Cancer Community
Finding Light Through Story-The Power of Ambassadorship in the Endometrial Cancer Community
*cancer that cannot be removed with surgery or has spread to other parts of the body. GEJ= gastroesophageal junction (where the esophagus joins the stomach)
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