According to GlobeNewswire, BridgeBio Pharmaceuticals and the Ivy Brain Tumor Center have recently began their Phase 0/2 trial of infigratinib. This treatment is meant for those with recurrent glioblastoma that…
The pandemic has made it difficult to get the same healthcare that we are used to. It is even harder for those who live with a medical condition or serious…
BioMarin has recently submitted a Marketing Authorization Application to the European Medicines Agency for their achondroplasia treatment, vosoritide. As of now, the review of the application will begin in August.…
The Michael J. Fox Foundation has awarded a grant of $750,000 to researchers at the University of California, Los Angeles for their work to improve the Parkinson's disease registry in…
Lupus nephritis causes kidney inflammation and can often lead to chronic kidney disease (CKD). An issue that medical professionals have faced is predicting the likelihood of individual patients developing CKD.…
According to Parkinson's News Today, an intestinal gel comprised of levodopa and carbidopa (LCIG) is able to lower the amount of time that Parkinson's patients spend in off episodes. These…
Orphazyme has recently submitted their New Drug Application to the FDA for their Niemann-Pick disease type C (NPC) treatment, arimoclomol. This application comes after the biopharmaceutical company was already granted…
A duodenoscope is a device used in endoscopic retrograde cholangiopancreatography (ERCP) procedures, in which a doctor uses them to see the top of the small intestine. For a long time,…
Khevin Barnes is a cancer survivor, as he won his battle with breast cancer. While less than one percent of breast cancer diagnoses are males, it is very important to…
Not much is known about the novel coronavirus; medical professionals are working to learn more every day. One of those things we are trying to understand is how this virus…
According to Ankylosing Spondylitis News, a new treatment, Hulio, has been approved by the FDA. It is a treatment for ankylosing spondylitis and other inflammatory disorders. Although it has been…
Living with a rare disease can come with some difficulties, whether those are physical, mental, or financial. It is estimated that 30 million Americans live with a rare disease, a…
According to Parkinson's News Today, the Parkinson's Foundation has released data from the PD GENEration study that shows that genetic testing is feasible for the larger Parkinson's community. As around…
The FDA has recently approved pembrolizumab, which is a treatment for colorectal cancer, specifically MSI-H and dMMR colorectal cancer. This approval comes after the release of positive results of the…
Data has recently been published to support a new diagnostic method for progressive supranuclear palsy, according to GlobeNewswire. Life Molecular Imaging and AC Immune SA have reported this data, which…
Diagnosing Parkinson's disease can be difficult, as it can only be done after motor symptoms appear. In an effort to create a better diagnostic method that can catch the disease…
A team of researchers from the University of Alberta have created a possible treatment for facioscapulohumeral muscular dystrophy (FSHD). Their work has been published in the Proceedings of the National Academy…
According to ASH Clinical News, a phase 1 trial of lenzilumab illustrated clinical benefits for approximately one third of participants with chronic myelomonocytic leukemia. It is a novel antibody, and…
There are multiple forms of Batten disease, each with their own distinct genetic cause. One of these forms is caused by a mutated CNL6 gene, but researchers were unsure as…
Vision loss is a major symptom of Stargardt disease, so a main goal of treatments is to combat this loss. In order to test the effectiveness of these treatments, there…
Medical professionals have found that the melatonin levels of Parkinson's patients impact their symptoms, specifically the gastrointestinal, sleep disturbance, and cardiac symptoms. Parkinson's News Today reported on a study that…
We are learning new things about COVID-19 every day. One of those things is the side effects, both neurological and physical. In fact, researchers from the UK have found that…
Researchers at Seelos Therapeutics are planning an animal study to evaluate SLS-007, a treatment for Parkinson's disease. According to an article from Parkinson's News Today, this study is possible after…
CytRx Corporation has released the results of the second phase of their study of arimoclomol as a treatment for Gaucher disease. The data was positive, and it demonstrated this therapy's…
Genentech has recently released the data from its SUNFISH trial, a study of the effects of risdiplam on spinal muscular atrophy (SMA) patients. Preliminary data from the JEWELFISH trial has…
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