Is CRISPR the Answer to Treating Progeria?
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Is CRISPR the Answer to Treating Progeria?

According to BioSpace, recent research has demonstrated that CRISPR gene editing could be the answer to treating progeria, or Hutchinson-Gilford progeria syndrome. The Broad Institute and NIH have collaborated to…

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Couple Adopts Child with Hemophilia
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Couple Adopts Child with Hemophilia

Monica and Josh Poynter have recently adopted a nine-year-old boy, Trey, from China. They felt a connection to the boy as he has hemophilia type A, the same rare bleeding…

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Report from the Neurological Alliance Calls for Improvements for Rare Neurological Disease Patients
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Report from the Neurological Alliance Calls for Improvements for Rare Neurological Disease Patients

The Neurological Alliance has released a report that details the experiences that rare, neurological disease patients in the UK share and calls for improvements for these people. Experts in the…

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Study: What is the Role of Fibrocytes and Endothelial Progenitor Cells in Lung Sarcoidosis?
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Study: What is the Role of Fibrocytes and Endothelial Progenitor Cells in Lung Sarcoidosis?

A study published in BMC Pulmonary Medicine focuses on the role of endothelial progenitor cells and fibrocytes in lung sarcoidosis. They specifically investigated how these cells, along with CD34 + cells, spurred…

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Health Canada Approves Hyrimoz for Ankylosing Spondylitis
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Health Canada Approves Hyrimoz for Ankylosing Spondylitis

According to GlobeNewswire, Health Canada has approved of a biosimilar, Hyrimoz, to treat ankylosing spondylitis and eight other rare conditions. Sandoz Canada is excited about this approval, as it expands…

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Initiation of Global Phase 3 Trial of Alagille Syndrome Treatment
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Initiation of Global Phase 3 Trial of Alagille Syndrome Treatment

Albireo has recently initiated their Phase 3 ASSERT trial, according to GlobeNewswire. This study will evaluate odevixibat as a treatment for Alagille syndrome. This therapy fits well with Albireo's mission,…

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