A Potential Methylmalonic Acidemia Therapy Will be Developed Under the FDA’s START Pilot Program
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A Potential Methylmalonic Acidemia Therapy Will be Developed Under the FDA’s START Pilot Program

Rare diseases are challenging. Not just for those affected, but for researchers, physicians, and drug developers. Rare diseases may affect small populations. Many are poorly understood and lack adequate awareness.…

Continue Reading A Potential Methylmalonic Acidemia Therapy Will be Developed Under the FDA’s START Pilot Program