Opfolda – Patient Worthy

Photo by Paweł Czerwiński on Unsplash

ICYMI: Opfolda for Pompe Disease Now Approved in the European Union

Post author:Jessica Lynn
Post published:July 22, 2023
Post category:Pompe Disease

In March 2023, the European Commission (EC) approved Pombiliti (cipaglucosidase alfa) for the treatment of adult patients living with late-onset Pompe disease. Just three months later in June, another…

CLICK HERE TO SHARE YOUR STORY!

We believe rare disease patients are people, not a diagnosis. Through education, awareness and some humor, we help patients, caregivers and support persons by providing relevant and often inspirational news and stories.

Our goals are to share stories, cultivate strong community, provide the latest medical findings, connect people and pioneer production of patient worthy information. Help us attain these goals by telling us a little bit about yourself!

ICYMI: Opfolda for Pompe Disease Now Approved in the European Union

Why Your Voice in Research Matters: Groundbreaking Studies are Changing What's Possible

Rethinking What It Means to Live With Acromegaly

The Let’s Chat CAR T One-on-One Mentor Program: Speaking with Someone Who Understands What You Are Going Through

Let’s Work Together!

Keep Up to Date

Learn More