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Rare Pediatric Disease Designation Awarded to Investigative Therapy for POMC and LEPR Deficiency Obesities

Post author:Trudy Horsting
Post published:July 13, 2020
Post category:Rare Disease

Rare pediatric disease designation has just been granted to Rhythm Pharmaceuticals for their investigative therapy called setmelanotide. This drug is being investigated as a therapeutic option for two conditions- leptin…

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