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132 Search Results Found

You searched for: "huntingtons"
Home » You searched for huntingtons

uniQure Receives FDA Fast Track Designation for AMT 130 Gene Therapy for the Treatment of Huntingtons Disease

LEXINGTON, Mass. and AMSTERDAM, the Netherlands - uniQure N.V. (NASDAQ: QURE), a leading gene therapy company advancing transformative therapies for patients with severe medical needs,  announced that the U.S. Food and Drug…

Continue Reading uniQure Receives FDA Fast Track Designation for AMT 130 Gene Therapy for the Treatment of Huntingtons Disease
Scientists Have Discovered An Immune Cell That May Partially Reverse Damage Caused by ALS and MS

Scientists Have Discovered An Immune Cell That May Partially Reverse Damage Caused by ALS and MS

A series of articles recently published in FierceBiotech describe a discovery by Ohio State and Michigan University scientists. The teams have discovered an immune cell that could be tapped to…

Continue Reading Scientists Have Discovered An Immune Cell That May Partially Reverse Damage Caused by ALS and MS
Juvenile Huntington’s Disease Linked to School and Social Problems

Juvenile Huntington’s Disease Linked to School and Social Problems

When children have problems at school, it is often linked to something bigger going on in another aspect of their life, whether that is at home or with friends. A…

Continue Reading Juvenile Huntington’s Disease Linked to School and Social Problems
Can Antihistamines Slow Huntington’s Disease Progression?

Can Antihistamines Slow Huntington’s Disease Progression?

by Lauren Taylor from In The Cloud Copy Huntington’s disease is an inherited disease that slowly causes the breakdown of the nerve cells of the brain, resulting in various disorders…

Continue Reading Can Antihistamines Slow Huntington’s Disease Progression?
Possible New Treatment for Facioscapulohumeral Muscular Dystrophy

Possible New Treatment for Facioscapulohumeral Muscular Dystrophy

A team of researchers from the University of Alberta have created a possible treatment for facioscapulohumeral muscular dystrophy (FSHD). Their work has been published in the Proceedings of the National Academy…

Continue Reading Possible New Treatment for Facioscapulohumeral Muscular Dystrophy
First Two Patients Treated with AMT-130 for Huntington’s Disease Trial

First Two Patients Treated with AMT-130 for Huntington’s Disease Trial

uniQure has recently began their Phase I/II clinical trial of AMT-130, a gene therapy for the treatment of Huntington's disease. Two patients are included so far, with one being given…

Continue Reading First Two Patients Treated with AMT-130 for Huntington’s Disease Trial
The Healthcare System Needs to Take Better Care of Black People

The Healthcare System Needs to Take Better Care of Black People

The events of the past week-- and the past few hundred years-- have brought up a lot of sadness, anger, and reckoning in our country. There are so many ways…

Continue Reading The Healthcare System Needs to Take Better Care of Black People
Exploring the Similar Pathology “Genetic Doppelgängers” ALS and SCA36

Exploring the Similar Pathology “Genetic Doppelgängers” ALS and SCA36

Recently, scientists from Emory University set out to discover whether there was any pathological link between spinocerebellar ataxia type 36 (SCA36) and amyotrophic lateral sclerosis and frontotemporal dementia (ALS/FTD). Both…

Continue Reading Exploring the Similar Pathology “Genetic Doppelgängers” ALS and SCA36
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