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Potential Treatment for Friedreich’s Ataxia Earns Orphan Drug and Rare Pediatric Disease Designations

Post author:James Moore
Post published:July 7, 2021
Post category:Friedreich ataxia Friedreich ataxia congenital glaucoma Friedreich's Ataxia Friedreich's ataxia

According to a story from GlobeNewswire, the gene therapy company LEXEO Therapeutics has recently announced that its investigational gene therapy LX2006 has been granted both Orphan Drug designation and Rare…

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