This Drug Saves Niemann-Pick Disease Type C Patients. It’s Being Pulled in Six Months.
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This Drug Saves Niemann-Pick Disease Type C Patients. It’s Being Pulled in Six Months.

According to a story from Scary Mommy, mother Sara McGlockin recently received devastating news: the drug that was successfully treating her five year old daughter Marian was being discontinued in…

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Ayvakit for Gastrointestinal Stromal Tumors Approved in China
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Ayvakit for Gastrointestinal Stromal Tumors Approved in China

According to a story from Markets Insider, the biopharmaceutical company CStone Pharmaceuticals has announced that China's National Medical Products Administration (NMPA) has approved avapritinib (marketed as Ayvakit) as a treatment…

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Experimental Hereditary Angioedema Treatment Performs Well in Phase 2 Trial
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Experimental Hereditary Angioedema Treatment Performs Well in Phase 2 Trial

According to a story from PR Newswire, the biotechnology company Ionis Pharmaceuticals recently announced promising findings from its phase 2 clinical trial. This clinical trial was evaluating the company's experimental…

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