This story contains images of severe lesions and blistering. On the weekend of October 12-14th of 2018, Patient Worthy had the privilege of attending the International Pemphigus & Pemphigoid Foundation's …
According to a story from finanznachrichten.de, the Korean biopharmaceutical company Biocure Technology, Inc., recently announced the results of a pre-clinical trial that tested CAR-T cell therapy as a treatment for acute…
According to a story from Healio, recent testing has found that FibroScan, a form of medical imaging, is capable of detecting nonalcoholic steatohepatitis earlier than it would be possible to…
According to a story from Market Screener, the pharmaceutical company Retrotope has recently released data that indicates that the company's experimental product RT001 is capable of halting disease progression for…
According to a story from EurekAlert!, a recent study from the University of Zurich has illuminated the connection between the gastrointestinal flora and multiple sclerosis. The discovery illuminates the potential…
According to a story from Charcot-Marie-Tooth News, a recent meeting between the US Food and Drug Administration (FDA) and patient advocacy groups took place to discuss the future development of…
According to a story from the New York Times, Harvard University has recently called for the retraction of 31 studies authored by a cardiologist associated with the school. The cardiologist…
According to a story from globenewswire.com, the biopharmaceutical company Orphazyme has officially endorsed a set of guidelines that outline how rare disease patient advocacy organizations and drug companies should interact…
According to a story from Pharma Voice, Dr. Scott Gottlieb, the current commissioner of the US Food and Drug Administration (FDA) has recently released a statement in regards to efforts…
According to a story from BioSpace, AstraZeneca and Merck released a joint announcement recently stating that the US Food and Drug Administration (FDA) has granted Orphan Drug designation to olaparib…
The Patient Advocate Foundation has recently begun to expand the reach of its popular Co-Pay Relief program. The Co-Pay Relief program is designed to provide financial assistance to qualifying patients.…
According to a story from baledezi.wordpress.com, a recent study demonstrated that a chemotherapy agent that originates from a sea sponge was able to prolong the lives of women with metastatic…
According to a story from pm360online.com, the orphan lung disease company Savara recently announced that they had completed their enrollment target of 135 patients for a Phase 3 clinical trial…
According to a story from Roche, the pharmaceutical company recently released new data from its ongoing clinical trial, which is testing the company's investigational product risdiplam. In this study, the…
According to a story from the Washington Post, new cases of the unusual, polio-like disease called acute flaccid myelitis have continued to appear through the United States recently. There are…
According to a story from BioSpace, the biotechnology company X4 Pharmaceuticals recently announced that the US Food and Drug Administration (FDA) has given Orphan Drug designation to the company's investigational…
According to a story from PR Newswire, a new program called The Lantern Project is working to provide a free testing program that allow doctors to more quickly diagnose patients…
According to a story from Bioportfolio, the biopharmaceutical company Newron Pharmaceuticals has chosen to support Rett Syndrome Awareness Month this year. Rett Syndrome Awareness Months falls on the October of…
According to a story from OncLive, the drug development company Karyopharm Therapeutics recently announced that the US Food and Drug Administration has granted Priority Review to the company's XPO1 inhibitor…
According to a story from news-medical.net, Verastem, Inc., recently announced that its drug COPIKTRA (duvelisib) was recently added to the National Comprehensive Cancer Network's (NCCN) guidelines for the treatment of…
Death or Debt? That is the question that begins the title of a recent study that is examining "financial toxicity" for patients with newly diagnosed cancer. Treatment for cancer is…
According to a story from PMLive, Leadiant Biosciences of Italy recently announced that its drug Revcovi has officially received approval from the US Food and Drug Administration. Revcovi was approved…
According to a story from Endpoints News, the Chief Science Officer for Spark Therapeutics is close to finishing up his first year with the company. His name is Federico Mingozzi,…
According to a story from Charcot-Marie-Tooth News, the continuously escalating cost of drugs in the United States is still plaguing rare disease patients and chronically ill people across the country.…
According to a story from mirror.co.uk, Lee and Charmaine Taggart of Kent are the parents of Martha, a six year old girl who was born with Angelman syndrome. Martha's diagnosis…
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