Events Search and Views Navigation
June 2017
March 2020
The Muscular Dystrophy Association’s Pompe Disease Patient-Focused Drug Development Meeting
Pompe Disease Patient-Focused Drug Development Meeting March 9th, 2020 This Patient-Focused Drug Development meeting is designed as a convergence of critical FDA officials, Pompe disease patients, pharmaceutical companies, and other relevant stakeholders for an important day of conversation about the future of Pompe disease treatment. This event will primarily feature patient testimony through panels and audience feedback related to the day to day challenges of living with this rare disease, as well as the goals that a future therapy for…
Find out more »