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The Muscular Dystrophy Association’s Pompe Disease Patient-Focused Drug Development Meeting
March 9 @ 8:00 am - 5:00 pm
Pompe Disease Patient-Focused Drug Development Meeting
March 9th, 2020
This Patient-Focused Drug Development meeting is designed as a convergence of critical FDA officials, Pompe disease patients, pharmaceutical companies, and other relevant stakeholders for an important day of conversation about the future of Pompe disease treatment.
This event will primarily feature patient testimony through panels and audience feedback related to the day to day challenges of living with this rare disease, as well as the goals that a future therapy for Pompe disease should aim to reach.
To register for this meeting, click here.