Patient Worthy

1 hour ago

Spinal muscular atrophy (SMA) is a condition that many people may not hear about often, but for those living with it, it’s part of daily life. Raising awareness helps create understanding — not just about the condition itself, but about the strength, resilience, and challenges that come with it.
Learning about SMA helps us build a more informed and compassionate community where people affected by rare diseases feel seen, supported, and understood. Every conversation, every shared fact, and every moment of awareness helps bring more visibility to a condition that deserves it.
#SpinalMuscularAtrophy #SMA #RareDiseaseOfTheWeek #RareDisease #RareDiseaseAwareness #PatientWorthy ... See MoreSee Less

Patient Worthy

3 hours ago

New research may offer hope for people living with #pku.

While still in development, this approach reflects growing momentum toward potentially durable, one-time genetic treatments for rare diseases.

patientworthy.com/2026/03/10/new-gene-editing-program-aims-to-address-root-cause-of-pku/ ... See MoreSee Less

Patient Worthy

5 hours ago

What is tardive dyskinesia? Keep reading to learn what this movement disorder is and what you need to know. Share your TD journey with us here: bit.ly/4dV7gru
#tardivedyskinesia #TDawareness #MentalHealthMatters #PatientWorthy ... See MoreSee Less