Patients suffering from sickle cell disease, SCD, might just be getting news they've been waiting to hear for a long time. Just this week, the U.S. Food and Drug Administration…
According to a story from philly.com, many people with severe forms of brain cancer are not receiving sufficient hospice treatment, according to a recent assessment. The study took data from…
Good news for patients who suffer from ankylosing spondylitis (AS). There may soon be a new option for treating their disease if the results of a new trial support the…
It's been two years since the Zika outbreak and now, two-year-olds born with microcephaly due to the infernal outbreak, are still suffering through long-term problems. Children who developed health problems…
Originally reported by The Straits Times, the Chew family from Singapore does everything they can to keep their nine-year-old daughter alive, even if it means spending their life savings and…
According to The Washington Post, on Tuesday the Food and Drug Administration, FDA, made history by approving a gene therapy for childhood blindness, which will change the lives of many…
As a scientist, Mary-Claire King has had a remarkable career related to her study of BRCA genes. She’s received a Lasker Award and has been recognized by President Obama with…
Great news for the rare disease community! Ultragenyx Pharmaceuticals reported back positive results from its phase 3 study of the treatment drug burosumab in adults with X-linked hypophosphatemia (XLH). XLH…
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