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amyotrophic lateral sclerosis (ALS) with SOD1 mutation

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Biogen’s Qalsody Receives UK Approval, Offering Hope for Rare Motor Neurone Disease

Biogen’s Qalsody Receives UK Approval, Offering Hope for Rare Motor Neurone Disease

  • Post author:Bree Clare
  • Post published:August 12, 2025
  • Post category:Motor neuron disease

Biogen has achieved a significant regulatory milestone with the UK Medicines and Healthcare products Regulatory Agency (MHRA) granting approval for Qalsody (tofersen), a treatment specifically developed for a rare and…

Continue Reading Biogen’s Qalsody Receives UK Approval, Offering Hope for Rare Motor Neurone Disease
ALS Patient Pleads With Biogen for the Chance to Extend Her Life Through Tofersen

ALS Patient Pleads With Biogen for the Chance to Extend Her Life Through Tofersen

  • Post author:Rose Duesterwald
  • Post published:March 30, 2021
  • Post category:Amyotrophic Lateral Sclerosis

Lisa Stockman Mauriello of Summit, New Jersey, is not alone in her struggle to gain access to the company’s experimental ALS drug, tofersen. In fact, according to a recent article…

Continue Reading ALS Patient Pleads With Biogen for the Chance to Extend Her Life Through Tofersen
Finding Light Through Story-The Power of Ambassadorship in the Endometrial Cancer Community
*cancer that cannot be removed with surgery or has spread to other parts of the body. GEJ= gastroesophageal junction (where the esophagus joins the stomach)
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