Rose became acquainted with Patient Worthy after her husband was diagnosed with Acute Myeloid Leukemia (AML) six years ago. During this period of partial remission, Rose researched investigational drugs to be prepared in the event of a relapse. Her husband died February 12, 2021 with a rare and unexplained occurrence of liver cancer possibly unrelated to AML.
Inflammatory bowel disease (IBD) affects approximately 1.6 million people in the U.S. According to a report in Healio, this equates to about 1.3% of the adult population. IBD can be…
A presenter at the COPD 2024 International Conference spoke about the ease with which heart failure and preserved ejection factor (HfpE) is misdiagnosed in COPD patients due to the similarity…
Sixty-six-year-old Tim Andrews, a resident of New Hampshire, is the fourth patient worldwide to undergo a pig kidney transplantation. As reported recently in a Mass General News Release, Tim is…
As reported in a recent edition of the Harvard Gazette, AI is commonly used to analyze X-rays and scans. AI has begun to outperform physicians in prognostic and diagnostic assessments.…
In June 2023 Jenny Decker took time out from her job as a trauma nurse and sailed out of Kona, Hawaii, beginning her solo voyage around the globe. Jenny’s mission…
This article is written by Enrico Orzes and originally published on Osservatorio Malattie Rare (OMaR). It has been translated from Italian. Patient Worthy is grateful to the team at OMaR…
Mesoblast Biotechnology Company has received FDA approval for its Ryoncil therapy as the first of its kind to be approved in the United States. The therapy has been developed to…
Sickle Cell, an inherited disease, involves crescent shaped red blood cells that are the “vehicles” containing hemoglobin, a protein responsible for carrying oxygen throughout the body. For almost a year…
Roche has been developing an experimental drug for Parkinson’s disease for over ten years. According to BioPharma Dive, the latest statements from the company are that the drug, prasinezumab, failed…
According to the data that was presented at the 2024 ACR Convergence, a considerable number of patients are hospitalized when it could have been avoided. As reported in Healio News,…
Approximately one and one half million people are affected by ulcerative colitis (UC) worldwide. It is an inflammatory bowel disorder with, as of yet, no known cause. There are, however,…
The FDA’s recent approval of AbbVie’s new combination therapy provides patients with longer-lasting control of movements. As described recently in Biopharmadive, Parkinson’s disease is characterized by uncontrolled muscle movements or…
The use of the gene therapy elivaldogene autotemcel (Skysona), has been approved due to its success in the treatment of patients diagnosed with the neurological disease cerebral adrenoleukodystrophy (CALD). The…
According to a recent report in Healio News, the GLP-1 agonists are medications developed primarily to control blood sugar levels for type two diabetes. About the FLOW Clinical Trial The…
Spinal muscular atrophy (SMA) is a rare disease causing progressive muscular weakness. Severe forms of the disease can be fatal to infants. Apitegromab is an experimental therapy that was successful…
Healio Gastroenterology Source: Concomitant use of common medications does not significantly affect UC induction therapy
Healio Cardiology Source: Immune checkpoint inhibitors for advanced lung cancer linked to higher blood clot risk
Eighty-five-year-old Frank Meuers considers his 500th immunoglobulin infusion to be a cause for celebration. Frank has logged details of his doctor’s visits since his first dose of replacement therapy with…
The Riken Center team, headed by Dr. Takaomi Saido and using mice with Alzheimer’s, discovered that dopamine may lessen the brain’s physical symptoms and improve memory. The study, featured in…
Fredericksburg, Virginia resident Johnny Boatman is a former national guardsman who had been in excellent physical condition all his life. That was until 2022 when he felt a sharp pain…
It has been almost a decade since the European medical community welcomed news of an innovation for primary biliary cholangitis (PBC). Therefore, the EC’s recent conditional approval of Ipsen’s drug…
In 2023 a 19-year-old male teenager was suffering from memory decline that first began when he was 17 years of age. His cognitive losses continued during the next few years.…
A protein called Aplp1 is now on the radar for its ability to spread material in the brain that may be responsible for Parkinson’s disease. Another protein, Lag3, interacts with…
Researchers discovered a version of the Cas protein that fits into adeno-associated viruses (AAVs). This virus can be engineered to deliver targeted therapy to cells and is a common approach…
Almost 100,000 people in the United States have been diagnosed with sickle cell disease (SCD). About one million people worldwide have the disease. Patients are at risk of death in…
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