Rose became acquainted with Patient Worthy after her husband was diagnosed with Acute Myeloid Leukemia (AML) six years ago. During this period of partial remission, Rose researched investigational drugs to be prepared in the event of a relapse. Her husband died February 12, 2021 with a rare and unexplained occurrence of liver cancer possibly unrelated to AML.

    Thalassemia and Sickle Cell Patients in the UK Gain Access to Blood Transfusion Test to Reduce Side Effects
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    Thalassemia and Sickle Cell Patients in the UK Gain Access to Blood Transfusion Test to Reduce Side Effects

    People living with blood disorders like sickle cell disease or thalassemia will now have access to a new blood test that will reduce transfusion side effects. England’s National Health Service…

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    Huntington’s Disease: Scientists Hope Their Success in Improving Survival in Mice Will Extend to Humans
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    Huntington’s Disease: Scientists Hope Their Success in Improving Survival in Mice Will Extend to Humans

    For years, scientists have been working on a completely new concept that generates new neurons in mice with Huntington's disease. They were able to demonstrate that the new cells could…

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    Xenotransplant: Study of Genetically Engineered Pig Kidney in the Human Body Offers Hope for Future Organ Supply
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    Xenotransplant: Study of Genetically Engineered Pig Kidney in the Human Body Offers Hope for Future Organ Supply

    Out of 103,000 people in the United States waiting for a transplant, almost 88,000 individuals on the waiting list need a kidney transplant. These statistics were recently provided through Organ…

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    Prilenia Therapeutics Announces Data Supporting Initiation of Phase III ALS Study
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    Prilenia Therapeutics Announces Data Supporting Initiation of Phase III ALS Study

    Prilenia Therapeutics, Waltham, Massachusetts and Naarden, Netherlands is a biotechnology company with a focus on developing therapeutics to treat neurodevelopmental disorders and neurodegenerative diseases. Prilenia presented data this month at…

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    Encouraging Results in Advanced Gastroenteropancreatic Neuroendocrine Tumors Phase III Trials
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    Encouraging Results in Advanced Gastroenteropancreatic Neuroendocrine Tumors Phase III Trials

    The primary outcome from the Phase III NETTER-2 clinical trial as reported recently in Globe Newswire, was heralded as extending progression free survival from 8.5 months to 22.8. The participants…

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    Sarepta is Pushing to Expand Duchenne Muscular Dystrophy Drug Label Despite Missed Endpoints
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    Sarepta is Pushing to Expand Duchenne Muscular Dystrophy Drug Label Despite Missed Endpoints

    Sarepta Therapeutics’ treatment Elevidys (delandistrogene moxeparvovec-rokl) received conditional approval from the FDA in June 2023. The designation implies that if the drug is used in accordance with its label, it…

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    Preventing Breast Cancer: Scientists Identify ‘Key’ to Potential Treatment and Prevention
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    Preventing Breast Cancer: Scientists Identify ‘Key’ to Potential Treatment and Prevention

    The immune system is constantly on the alert for cells that have sustained DNA damage. When a cell divides its DNA molecules are, to varying degrees, usually damaged. Yet researchers…

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    Research Breakthrough: Scientists May Have Discovered How Tumor Cells Outwit the Immune System
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    Research Breakthrough: Scientists May Have Discovered How Tumor Cells Outwit the Immune System

    Editor's Note: Chronic conditions and rare diseases don't discriminate, Patient Worthy and its partners are interested in amplifying the voices of those from all identities and backgrounds. If you have…

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    Does Brain Inflammation Play a Role in Alzheimer’s Disease?
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    Does Brain Inflammation Play a Role in Alzheimer’s Disease?

    Neurogeneticist Michael Nalls of the US National Institute on Aging recently told Science Alert that a 2022 study, published in the Journal of Alzheimer’s Disease, completely changed their discovery approach.…

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    Carisma Therapeutics is Developing CT-0508 to Target HER2 Positive Cancers
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    Carisma Therapeutics is Developing CT-0508 to Target HER2 Positive Cancers

    Carisma Therapeutics, the manufacturer of CT-0508, issued a press release stating that researchers are conducting a combination study using CAR-M cell therapy plus Keytruda (pembrolizumab) in the treatment of overexpressing…

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