A recent research article in ScienceDirect.com details a breakthrough in visualizing the rapid, complex movements of proteins using high-speed atomic force microscopy (HS-AFM). This cutting-edge imaging technology allows scientists to…
A recent case report has brought attention to a rare but potentially life-threatening cause of heart attack: spontaneous coronary artery dissection (SCAD) in a young woman without classic risk factors…
Madrigal Pharmaceuticals is making significant strides in its mission to address metabolic dysfunction-associated steatohepatitis (MASH), as the company’s lead drug, REZDIFFRA, edges closer to regulatory approval in the European Union.…
A recently published case report has shed light on an uncommon cause of abdominal pain in adults: small bowel intussusception due to a benign tumor known as a lipoma. As…
A groundbreaking clinical milestone has been reached in gastroenterology with the publication of a first-in-human study evaluating a novel spray gel for the treatment of ulcers following endoscopic submucosal dissection…
A significant milestone has been achieved in the fight against blood cancers, as the first patient has been dosed in a pivotal Phase 3 clinical trial evaluating a promising new…
In a remarkable stride toward personalized cancer treatment, scientists have developed a groundbreaking test designed to predict whether individual patients will respond to chemotherapy or develop resistance. According to Bioengineering.com,…
Go here to read Part 1, Part 2, and Part 3 of this series provided by TREND Community about Prader-Willi Syndrome. In January 2025, the TREND Community published another comprehensive report…
The treatment landscape for hemophilia B has taken a historic leap forward, as the first patient in the UK’s National Health Service (NHS) has received Hemgenix, a pioneering gene therapy…
Madrigal Pharmaceuticals has recently captured significant attention in the race to treat metabolic dysfunction-associated steatohepatitis (MASH), formerly known as nonalcoholic steatohepatitis (NASH). As the landscape of liver disease therapeutics evolves,…
As reported by HD Buzz, a significant step forward for Huntington’s disease (HD) research, Roche has announced that the first patient has been dosed in its new gene therapy clinical…
Anixa Biosciences has reached a new milestone in the development of its innovative CAR-T cell therapy, announcing the dosing of the first patient in the fourth cohort of its ongoing…
In a moving story of resilience and hope, a 10-year-old patient is embracing a new lease on life after receiving a heart transplant, seen as a medical miracle that has…
A significant milestone has been reached in multiple sclerosis (MS) research with the imaging of the first patient in a clinical trial using a novel PET tracer. This innovative approach…
Not everyone who stands up for children’s health in Washington, DC, wears a suit or carries a briefcase. Sometimes, the most powerful advocates are the ones who have experienced the…
The world of healthcare is changing rapidly, and technology is at the heart of its evolution. The latest innovation making waves is an AI-powered medical receptionist that’s not only efficient…
Patient Worthy is grateful to our partner Elephants & Tea for providing the following article by Laura DeKraker Lang-Ree, a cancer caregiver to her daughter Cecilia who survived childhood leukemia.…
Mama we are all different colors and we are all beautiful. For our final Throwback Thursday we bring to you the story of Mariana, a young girl diagnosed with Pfeiffer…
In a remarkable demonstration of medical innovation, a Florida-based surgeon recently performed a robotic surgery on a patient located over 7,000 miles away. This groundbreaking procedure highlights the immense potential…
Cure Rare Disease (CRD), a pioneering nonprofit biotechnology organization, has announced the addition of new scientific and strategic leaders, marking a significant step forward in its mission to develop therapies…
Go here to read Part 1 and Part 2 of this series provided by TREND Community about Prader-Willi Syndrome. TREND Community released a revealing report in November 2024 titled “Pulse…
A recent article from Free Malaysia Today tells the remarkable story of Shu Hua, a woman who has not only surpassed a dire prognosis but continues to inspire others with…
In the vast world of podcasts, “Wait, How Do You Spell That?” stands out as a beacon for patients, families, and advocates navigating the complex, often isolating journey of rare…
A new study published at ScienceDirect.com sheds light on the profound social challenges faced by individuals and families living with rare diseases. The article examines how rare diseases, while medically…
A recent report from the Times of India tells the inspiring story of a serving Indian Army soldier who overcame a critical health battle thanks to a successful lung transplant…
Sign Up With a Patient Worthy Account and Share Your Rare Story
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
