According to a recent article, a new study from Boston Children’s Hospital shows that a first-of-its-kind gene therapy technique has succeeded in reversing severe hearing loss from a mutation to…
There rare disease world has another rising hope in research and development. Her name is Christina Waters, and she is the founder and CEO of Rare Science, a California non-profit…
Allison and Ben Gauvin have been to hell and back, but they manage to keep their spirits up. The couple from Connecticut lost their two children to a rare mitochondrial…
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