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Investigative Gene Therapy for Canavan Disease has Been Given Three New Designations by the FDA

Investigative Gene Therapy for Canavan Disease has Been Given Three New Designations by the FDA

  • Post author:Trudy Horsting
  • Post published:April 4, 2022
  • Post category:Canavan disease

Myrtelle Inc. has just announced that they have been granted three new designations from the FDA for their investigative gene therapy called rAAV-Olig001-ASPA. This therapy is being investigated as a…

Continue Reading Investigative Gene Therapy for Canavan Disease has Been Given Three New Designations by the FDA
Myrtelle Announces the First-in-Human Trial of a Targeted Gene Therapy for Canavan Disease (CD)

Myrtelle Announces the First-in-Human Trial of a Targeted Gene Therapy for Canavan Disease (CD)

  • Post author:Rose Duesterwald
  • Post published:March 10, 2022
  • Post category:Canavan disease

Myrtelle, via Business Wire News, reports the completion of Phase 1/2 investigating its gene therapy for Canavan disease (CD) which they have now expanded to treat younger patients. Thus far,…

Continue Reading Myrtelle Announces the First-in-Human Trial of a Targeted Gene Therapy for Canavan Disease (CD)
Cushing’s Disease News Guaranteed to Get You Excited
[Source: pixabay.com]

Cushing’s Disease News Guaranteed to Get You Excited

  • Post author:Alisha Stone
  • Post published:October 4, 2016
  • Post category:Cushing Disease/Rare Disease

Yowzaaa! You don’t want to miss the article by Jeannette Y. Wicks, RPh, MBA, FASCP about Cushing’s disease (CD). Cushing's is a rare disease that’s caused by high levels of…

Continue Reading Cushing’s Disease News Guaranteed to Get You Excited
Finding Light Through Story-The Power of Ambassadorship in the Endometrial Cancer Community
*cancer that cannot be removed with surgery or has spread to other parts of the body. GEJ= gastroesophageal junction (where the esophagus joins the stomach)
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