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GTX-102

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Patient Enrollment Begins in GTX-102 Trial for Angelman Syndrome
rawpixel / Pixabay

Patient Enrollment Begins in GTX-102 Trial for Angelman Syndrome

  • Post author:Jessica Lynn
  • Post published:May 21, 2021
  • Post category:Angelman Syndrome

In a news release from May 19, 2021, startup biotechnology company GeneTx Biotherapeutics LLC ("GeneTx") and biopharmaceutical company Ultragenyx Pharmaceutical Inc. ("Ultragenyx") shared that the pair received Health Canada clearance…

Continue Reading Patient Enrollment Begins in GTX-102 Trial for Angelman Syndrome
GTX-102 to Treat Angelman Syndrome Given Fast Track Designation
source: pixabay.com

GTX-102 to Treat Angelman Syndrome Given Fast Track Designation

  • Post author:Jessica Lynn
  • Post published:May 21, 2020
  • Post category:Angelman Syndrome

  A recent news release on BioSpace shares how GTX-102, an investigational antisense oligonucleotide drug therapy for Angelman syndrome, was granted Fast Track designation from the FDA. The therapy, created by GeneTx…

Continue Reading GTX-102 to Treat Angelman Syndrome Given Fast Track Designation
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