phenyketonuria – Patient Worthy

Preclinical Findings for Phenylketonuria and Metachromatic Leukodystrophy Gene Therapies Look Promising

Post author:James Moore
Post published:October 29, 2019
Post category:Metachromatic Leukodystrophy Phenylketonuria pku

According to a story from BioSpace, the genetic medicines company Homology Medicines, Inc., has recently released preclinical data supporting the development of two experimental gene therapies. One, called HMI-202, is…

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