RPE65 mutation – Patient Worthy

When Can Gene Therapy Treat Leber Congenital Amaurosis for Good?

Post author:Sunniva Bean
Post published:September 23, 2019
Post category:Leber Congenital Amaurosis Rare Disease

Genes themselves are a relatively new discovery, found only about a century ago. Gene therapy, a medical procedure that alters genes to address disease, is a concept a few decades…

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When Can Gene Therapy Treat Inherited Blindness Longterm?

Post author:Sunniva Bean
Post published:September 16, 2019
Post category:Rare Disease

Genes themselves are a relatively new discovery, found only about a century ago. Gene therapy, a medical procedure that alters genes to address disease, is in its first 30 years.…

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