RT001 – Patient Worthy

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RT001 Granted Rare Pediatric Disease Designation for INAD, FA

Post author:Jessica Lynn
Post published:March 22, 2021
Post category:Friedreich ataxia Friedreich's Ataxia Infantile axonal neuropathy

In a press release from late February 2021, biopharmaceutical company Retrotope shared that its lead drug candidate, RT001, received Rare Pediatric Disease designation for the treatment of patients with Friedreich's…

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