October 22, 2015 – Patient Worthy

Her Near Death Meant New Hope for 6-Year-Old Son

Post author:Kiki Jones
Post published:October 22, 2015
Post category:CAPS Rare Disease

We all know that an early diagnosis can save lives. But, in an unexpected turn, this mother’s late diagnosis is what saved her son. RareConnect.org details the story of Malinda…

source: pixabay.com

A Promising New Acromegaly Drug Awaits FDA Blessing

Post author:Ronald Ledsen
Post published:October 22, 2015
Post category:Acromegaly Rare Disease

If you’re one of the small number of people living with acromegaly symptoms today (an estimated 60 out of every million people worldwide), we’ve got some good news for you.…

Here’s Something About Bubble Boy That You Never Knew

Post author:Ronald Ledsen
Post published:October 22, 2015
Post category:Primary Immunodeficiencies Rare Disease SCID

For those of us who grew up in the 1970s and 1980s, the phrase “Bubble Boy” zaps us right back to a sharp mental image that will always stick with…

The FDA Just Gained Big Brownie Points from Rare Disease Patients

Post author:Winnie Nash
Post published:October 22, 2015
Post category:Rare Disease

Earlier this year, the FDA took bold steps, launching them closer to efficient rare disease drug development. And now, the potential improvement for rare disease patients could be huge. Why?…

Her Near Death Meant New Hope for 6-Year-Old Son

A Promising New Acromegaly Drug Awaits FDA Blessing

Here’s Something About Bubble Boy That You Never Knew

The FDA Just Gained Big Brownie Points from Rare Disease Patients

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