Earlier this week, a press release from Alnylam Pharmaceuticals, Inc, announced the that the phase 3 study of their experimental acute hepatic porphyria drug Givosiran yielded positive results. According to the…
A publication from OncLive recently reported that the FDA has granted the experimental myelofibrosis drug Fedratinib a priority review designation, following Celgene Corporation's submission of a New Drug Application (NDA) to the…
A recent press release from the French biopharmaceutical company Inventiva announced that the Food and Drug Administration (FDA) had granted the company's experimental mucopolysaccharidosis VI (MPS VI) drug odiparcil rare…
According to a news wire from Sound Pharmaceuticals, the biotechnology company has completed patient enrollment for its Phase 2b clinical trial involving Meniere's disease. About Meniere's Disease Meniere's disease (MD)…
According to a publication from MarketWatch, many people living with cancer are going broke just trying to stay alive. Millennials seem to be particularly vulnerable to falling into a self-perpetuating…
According to a story from the Breast Cancer Society of Canada, Veronica Dubois, who is currently pursuing a Master of Science in Medical Biophysics, is focusing her research on developing…
In the early 1900s, German psychiatrist Alois Alzheimer, while studying about the decline in brain function, recognized a correlation between behavioral changes and the buildup of tangles and plaques in…
This week, a publication from BioSpace announced that a second individual has been cleared of HIV in another astounding success for stem cell therapy. The individual known only as the…
Wisconsin; the land of beer, cheese, good-hearted people, and Maria Voermans - rare cancer survivor and now fierce advocate for the rare disease community. Ten years ago, Maria had the…
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