Editor’s Choice: Approvals and Disappointments in Rare Research News

Happy Thursday Everyone!

We hope everyone’s spring is off to a good start! This week, we’re highlighting four articles about research updates. We have news pertaining to Methylmalonic Acidemia patients and families followed by an update on Hemophilia A treatment research. Next, we have news on a trial discontinuation as well as a Multiple Myeloma approval in England.

Sit back and enjoy this week’s Editor’s Choice.

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NIH Works With Patients and Families on Methylmalonic Acidemia Research

The NIH is taking steps to involve the communities affected by this rare disease.

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Preventive Use of Extended Half-Life Therapies Provides Enhanced Benefit for Hemophilia A Patients

Research shows this treatment could help Hemophilia A patients prevent bleeds before they happen.
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Phase III Ovarian Cancer Clinical Trial to be Discontinued

Ovarian cancer treatment development experiences a setback.

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New Combination Therapy for Multiple Myeloma Approved in England

Our friends across the pond have new treatment options for Multiple Myeloma.

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Do you have a rare disease experience of your own? Share with us here.

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