June 2024 – Page 3 – Patient Worthy

Rare Community Profiles: #RAREis: Advancing Clinical Trial and Patient Equity with the Foundation for Sarcoidosis Research’s Mary McGowan

Post author:Jessica Lynn
Post published:June 4, 2024
Post category:Sarcoidosis

Rare Community Profiles is a Patient Worthy article series of long-form interviews featuring various stakeholders in the rare disease community, such as patients, their families, advocates, scientists, and more.…

source: pixabay.com

Transfusions with Contaminated Blood Mean 1750 People in the UK Have Undiagnosed Hepatitis C

Post author:Jessica Lynn
Post published:June 3, 2024
Post category:Hepatitis C

Blood transfusions are a vital medical procedure used to address a multitude of health conditions and emergencies, such as severe anemia, sepsis, trauma, internal bleeding, hemophilia, sickle cell disease, thalassemia,…

source: shutterstock.com

ASGCT: Clinical Data Shows Favorable Profile of FLT201 for Gaucher Disease

Post author:Jessica Lynn
Post published:June 3, 2024
Post category:Gaucher Disease

The American Society of Gene and Cell Therapy (ASGCT) held its 27th Annual Meeting from May 7-11, 2024. During the conference, stakeholders in the field of cell therapy come together…

source: shutterstock.com

ASO Therapy Improves Cellular Function in Timothy Syndrome Brain Organoids

Post author:Jessica Lynn
Post published:June 3, 2024
Post category:Long QT Syndrome Timothy syndrome

Have you heard of antisense oligonucleotides (ASOs)? These short, synthetic strands of nucleic acids are designed to bind specifically to the mRNA transcripts of genes, blocking the production of disease-causing…

Rare Community Profiles: #RAREis: Advancing Clinical Trial and Patient Equity with the Foundation for Sarcoidosis Research’s Mary McGowan

Transfusions with Contaminated Blood Mean 1750 People in the UK Have Undiagnosed Hepatitis C

ASGCT: Clinical Data Shows Favorable Profile of FLT201 for Gaucher Disease

ASO Therapy Improves Cellular Function in Timothy Syndrome Brain Organoids

Let’s Work Together!

Keep Up to Date

Learn More