December 19, 2024 – Patient Worthy

source: shutterstock.com

Gene Therapy Promising for Cerebral Adrenoleukodystrophy but Carries Risk of Blood Cancer

Post author:Rose Duesterwald
Post published:December 19, 2024
Post category:Adrenoleukodystrophy

The use of the gene therapy elivaldogene autotemcel (Skysona), has been approved due to its success in the treatment of patients diagnosed with the neurological disease cerebral adrenoleukodystrophy (CALD). The…

We believe rare disease patients are people, not a diagnosis. Through education, awareness and some humor, we help patients, caregivers and support persons by providing relevant and often inspirational news and stories.

Our goals are to share stories, cultivate strong community, provide the latest medical findings, connect people and pioneer production of patient worthy information. Help us attain these goals by telling us a little bit about yourself!

Let’s Work Together!

Keep Up to Date

Learn More