Madrigal Pharmaceuticals has recently captured significant attention in the race to treat metabolic dysfunction-associated steatohepatitis (MASH), formerly known as nonalcoholic steatohepatitis (NASH). As the landscape
A significant milestone has been achieved in the fight against blood cancers, as the first patient has been dosed in a pivotal Phase 3 clinical
In a remarkable stride toward personalized cancer treatment, scientists have developed a groundbreaking test designed to predict whether individual patients will respond to chemotherapy or
Editor’s Note: This article was originally published by Patient Worthy on 6/7/2017, and is being republished due to current NASH/MASH awareness efforts. If you would
I often find myself initially stuck on where to start when telling our story. I say “our” because that’s the truth of this rare disease
Go here to read Part 1, Part 2, and Part 3 of this series provided by TREND Community about Prader-Willi Syndrome. In January 2025, the TREND
The treatment landscape for hemophilia B has taken a historic leap forward, as the first patient in the UK’s National Health Service (NHS) has received
As reported by HD Buzz, a significant step forward for Huntington’s disease (HD) research, Roche has announced that the first patient has been dosed in
Editor’s Note: Patient Worthy is honored to bring you this article originally authored by Shannon Cloud, Patient Advocacy Director of the Dravet Syndrome Foundation. A
Anixa Biosciences has reached a new milestone in the development of its innovative CAR-T cell therapy, announcing the dosing of the first patient in the
In a moving story of resilience and hope, a 10-year-old patient is embracing a new lease on life after receiving a heart transplant, seen as
A significant milestone has been reached in multiple sclerosis (MS) research with the imaging of the first patient in a clinical trial using a novel
Not everyone who stands up for children’s health in Washington, DC, wears a suit or carries a briefcase. Sometimes, the most powerful advocates are the
The world of healthcare is changing rapidly, and technology is at the heart of its evolution. The latest innovation making waves is an AI-powered medical
Global biotechnology leader CSL recently announced the FDA’s approval of ANDEMBRY, a monthly subcutaneous (under-the-skin) self-injection. The treatment was recently FDA approved for the prevention
Patient Worthy is grateful to our partner Elephants & Tea for providing the following article by Laura DeKraker Lang-Ree, a cancer caregiver to her daughter
Mama we are all different colors and we are all beautiful. For our final Throwback Thursday we bring to you the story of Mariana, a
In a remarkable demonstration of medical innovation, a Florida-based surgeon recently performed a robotic surgery on a patient located over 7,000 miles away. This groundbreaking
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