Rare Disease
Editors Choice: Rare Disease Round Up
Happy Almost-Friday! This week, we’re highlighting two organizations: one helps patients seeking gene therapy learn about the treatments, and the other helps families affected by
Rare Patient News. Well Done.
Recent Advances put a Cure for Cushing’s Disease in Striking Distance
- February 21, 2020
Elderly Patients with Myelodysplastic Syndromes can Have Successful Transplants
Four Tips for Coping with a Chronic Illness
Can PharmaCyte’s “Cell-in-a-Box” be a Breakthrough for Pancreatic Cancer?
LATEST PATIENT WORTHY ARTICLES
Spinal Muscular Atrophy
A College Student Started a Business to Inspire Others with Spinal Muscular Atrophy
One of the wealthy regulars on the TV show Shark Tank made his millions by starting a home-based business selling tee shirts. An article
Rare Disease
US Senate Considers Legislation for Kids’ Rare Disease Whole Genome Sequencing
By Jodee Redmond from In The Cloud Copy Four United States senators have introduced a new law that, if passed, will assist children living with
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Amyotrophic Lateral Sclerosis
A Phase 3 Entry In the Race To Save ALS Patients
ALS News Today recently announced the introduction of a Phase 3 clinical trial for oral edaravone, a drug that has previously been approved for
Lyme Disease
Documentary Investigates the Controversy of Morgellons Disease
The validity of Morgellons disease, which has been associated with Lyme disease, has been widely debated for years. Those affected by it swear that it
Progeria
Progeria: Cam and Cam Meet Face to Face
By Danielle Bradshaw from In The Cloud Copy 13-year-old Cam Howard, a young Pittsburgh resident, recently did an interview with the Pittsburgh KDKA News’ Kristine
