Study Finds That BRAF Inhibitors Could be an Effective Treatment for Some Ovarian Cancer Patients

JMoore - August 18, 2018

Autosomal Dominant Polycystic Kidney Disease

The Burden of PKD: A Patient Story

Cystic FibrosisFabry DiseaseMultiple SclerosisSpinal Muscular Atrophy

So Why DOES Canada have Scarcer Access to Rare Disease Therapies?

Brain Cancer

Pediatric Cancer Rates are Highest in the Northeast, But No One Knows Why

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GNE Myopathy

Register Now to Attend the Symposium on GNE Myopathy for Free!

Calling all members of the GNE Myopathy community! The Neuromuscular Disease Foundation (NDF) is hosting its 5th Annual Symposium on GNE Myopathy this August 30-31st at the University

Primary Immunodeficiencies

Epigenetic Technology Could Become Useful in Newborn Screening for Primary Immunodeficiency and Monitoring HIV

Researchers are exploring a new diagnostic method that could be applied to newborn screening for certain inherited diseases and monitoring of HIV patients. For more

Familial Chylomicronemia Syndrome

Results from First Study on Patient-To-Patient Connectivity in Those with FCS

According to DAIC, Akcea Therapeutics Inc., has recently announced their publication of results from their study analyzing patient-to-patient connectivity towards the management of the

Aicardi Syndrome

At Just Weeks Old, a Baby From Auckland is Diagnosed With Aicardi Syndrome and Opsoclonus Myoclonus Syndrome

According to a story from stuff.co.nz, a baby from Auckland has been diagnosed with two extremely rare disorders that only occur in one in every

Cystic Fibrosis

A Historic New Discovery Could Have Major Implications for Cystic Fibrosis

According to a story from Science Alert, the human body is a grand and complex natural structure. While it is easy to think of the

Ewing's family of tumors

The FDA Has Granted Rare Pediatric Disease Designation to an Investigational Drug For the Treatment of Ewing’s Sarcoma

9% Copyscape An investigational drug called CLR 131 has received Rare Pediatric Disease Designation from the US FDA for the treatment of Ewing’s sarcoma. The

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TRENDING NOW ON PATIENT WORTHY

POTS and Vasovagal Syncope: A Patient Story - Community Spotlight, POTS, Vasovagal syncope

A Historic New Discovery Could Have Major Implications for Cystic Fibrosis - Cystic Fibrosis, Rare disease, Research

Teenager with Rare Disease Treks Across the Country with a Very Important Message - Primary periodic paralysis, Rare disease, Ride for Rare Diseases, Sponsored

Study Finds That BRAF Inhibitors Could be an Effective Treatment for Some Ovarian Cancer Patients

The Burden of PKD: A Patient Story

So Why DOES Canada have Scarcer Access to Rare Disease Therapies?

Pediatric Cancer Rates are Highest in the Northeast, But No One Knows Why

LATEST PATIENT WORTHY ARTICLES

Register Now to Attend the Symposium on GNE Myopathy for Free!

Epigenetic Technology Could Become Useful in Newborn Screening for Primary Immunodeficiency and Monitoring HIV

Results from First Study on Patient-To-Patient Connectivity in Those with FCS

At Just Weeks Old, a Baby From Auckland is Diagnosed With Aicardi Syndrome and Opsoclonus Myoclonus Syndrome

A Historic New Discovery Could Have Major Implications for Cystic Fibrosis

The FDA Has Granted Rare Pediatric Disease Designation to an Investigational Drug For the Treatment of Ewing’s Sarcoma

UPCOMING EVENTS

2018 Scleroderma Foundation National Patient Education Conference

The Periodic Paralysis Association’s 2018 Conference

The National Fabry Disease Foundation’s Fabry Family Education Conference

The Myositis Association’s Annual Patient Conference

The Coffin-Siris Syndrome Foundation’s Conference 2018

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TRENDING NOW ON PATIENT WORTHY

POTS and Vasovagal Syncope: A Patient Story - Community Spotlight, POTS, Vasovagal syncope

A Historic New Discovery Could Have Major Implications for Cystic Fibrosis - Cystic Fibrosis, Rare disease, Research

Teenager with Rare Disease Treks Across the Country with a Very Important Message - Primary periodic paralysis, Rare disease, Ride for Rare Diseases, Sponsored

A Woman With Vulvar Cancer Has a Terminal Prognosis. Now She is Spreading Awareness - Community Spotlight, Lichen Sclerosus, Vulvar cancer

Study Finds that Prognosis for Systemic Sclerosis can be Predicted with this Simple Test - Rare disease, Research, Scleroderma, Systemic sclerosis

The Dos and Don'ts of Exercising with Ehlers-Danlos Syndrome - EDS, Ehlers-Danlos syndrome, Hypermobility, Opinion, Resource

How Getting Diagnosed With POTS Changed My Life: A Patient Story - Community Spotlight, Dysautonomia, POTS, Rare disease

10 consejos alimenticios para el Síndrome de Sjögren - Anti-inflammatory diet, Espanol, News, Rare disease, Sjogren's

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