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PATIENT WORTHY SERIES

Study of the Week: A New Treatment Option for Lupus?

Welcome to Study of the Week from Patient Worthy. In this segment, we select a study we posted about from the previous week that we

Rare Classroom: Alternating Hemiplegia of Childhood

Welcome to the Rare Classroom, a new series from Patient Worthy. Rare Classroom is designed for the curious reader who wants to get informed on

GACI/ARHR2 Awareness Day is February 1st: Spreading rare Disease Awareness

Generalized arterial calcification of infancy (GACI) and autosomal recessive hypophosphatemia rickets type 2 (ARHR2) Awareness Day is recognized each year on Feb 1. This is

Study of the Week: A new Approach to Treat Mitochondrial Disease

Welcome to Study of the Week from Patient Worthy. In this segment, we select a study we posted about from the previous week that we

MPS VI (Maroteaux-Lamy syndrome)

Maroteaux-Lamy Syndrome Patient Facing Deportation can now Stay in the US

According to a story from the East Bay Times, it was 2003 when Isabel Bueso and her family traveled to the US from Guatemala. She

Peripheral T-cell lymphoma

EC Grants Orphan Status to Duvelisib for PTCL

In the European Union (EU), Orphan designation, or Orphan Medicinal Product designation, is granted to drugs or biologics intending to treat, diagnose, or prevent

Superior Mesenteric Artery Syndrome

Help Raise Funds for Teen with Superior Mesenteric Artery Syndrome

In March 2022, T. Kavinraj began experiencing a number of worrying health symptoms. He had a splitting headache and could not stop vomiting. In fact,

Pancreatic Cancer

QN-302 Granted Orphan Drug Designation for Pancreatic Cancer

In the United States, the Food and Drug Administration (FDA) grants Orphan Drug designation to drugs or biologics which intend to treat, diagnose, or prevent

Mitochondrial Disease

Mitochondrial Transplants from Mothers: A Controversial idea Evolves into a Potential Remedy for Mitochondrial Disease

Ten years ago, a biochemist was seeking investors for her new company that was developing mitochondrial-based medicines. The Israeli-born embryologist observed how the blending

Moebius Syndrome

January 24 is Moebius Syndrome Awareness Day!

This year, the 13th annual Moebius Syndrome Awareness Day (MSAD) will take place on Tuesday, January 24. Moebius Syndrome Awareness Day, as the name suggests,

Syringomelia hyperkeratosis

Rare Classroom: Syringomelia

Welcome to the Rare Classroom, a new series from Patient Worthy. Rare Classroom is designed for the curious reader who wants to get informed on

Graft versus Host Disease

AltruBio’s Dr. Jesse Hall Discusses Data on ALTB-168 for Acute GvHD

The American Society of Hematology (ASH) held its 64th Annual Meeting from December 10-13, 2022. During the meeting, doctors, researchers, and other stakeholders within the

Lip and oral cavity cancer

A Biosensor Could Improve Lip and Oral Cavity Cancer Diagnosis

In multiple disease states, early identification, diagnosis, and treatment can significantly improve overall survival rate and patient outcomes. This is especially true for lip and

Narcolepsy

A Mental Health Counselor Discusses His Life with Narcolepsy

Chris was tired. Not just tired, actually, but fatigued. Normally, he loved working with his clients as a mental health counselor—and in his spare time,